-
2024-511925-71-00
5
2021-08-05
Acromegaly
-
2024-513672-17-00
4
2021-06-14
Inoperable Chronic thromboembolic pulmonary hyperTension
-
2024-512123-37-00
5
2021-05-27
Parkinson's disease
-
2023-506918-45-00
5
2021-05-17
Mild cognitive impairment (MCI) or mild dementia, both of the Alzheime
-
2023-506919-18-00
5
2021-05-17
Mild cognitive impairment (MCI) or mild dementia, both of the Alzheime
-
2023-507317-10-00
5
2021-05-10
Locally advanced, unresectable, or metastatic non small cell lung canc
-
2024-513856-14-00
6
2021-05-05
Patients with high-grade serous epithelial ovarian, tubal or primary p
-
2024-516431-27-00
6
2021-02-23
Wilson’s Disease
-
2023-507850-33-00
5
2021-02-05
Hematopoietic stem cell transplant-associated thrombotic microangiopat
-
2024-514495-41-00
5
2020-11-04
Primary Progressive Multiple Sclerosis
-
2024-515943-44-00
4
2020-10-14
Non small cell lung cancer
-
2023-505035-12-00
5
2020-06-12
RET fusion−positive, metastatic Non-Small Cell Lung Cancer
-
2024-511427-34-00
5
2020-02-20
idiopathic pulmonary fibrosis
-
2023-503382-29-00
5
2020-01-20
Primary Hyperoxaluria Type 1 (PH1)
-
2023-503673-38-00
5
2019-05-24
Adults at high risk of cardiovascular events without prior MI or strok
-
2023-509304-16-00
5
2019-05-16
Pulmonary arterial hypertension (PAH)
-
2024-510751-34-00
5
2019-03-26
Gaucher's disease type I; Gaucher's disease type III
-
2023-506543-41-00
5
2018-07-25
Multiple sclerosis (MS)
-
2023-506739-14-00
4
2017-05-12
Spinal Muscular Atrophy (SMA)
-
2023-509137-39-00
5
2015-11-06
Stage IB (T ≥ 4 cm), II and IIIA NSCLC
-
2024-514403-34-00
9
2012-10-10
Late Metachromatic Leukodystrophy (MLD)
-
2022-500302-18-00
4
Epilepsy
-
2023-503926-37-00
10
Biliary Atresia, Post-hepatoportoenterostomy
-
2023-509615-92-00
4
Ischemic stroke with Large Core