-
2024-519579-24-00
5
2026-02-26
Classic Congenital Adrenal Hyperplasia
-
2024-519068-42-00
10
2026-02-12
Heterozygous Familial Hypercholesterolemia in pediatric patients
-
2025-521558-40-00
5
2026-02-12
Pulmonary Hypertension Associated with Interstitial Lung Disease
-
2024-512261-14-00
4
2025-12-22
Hypochondroplasia
-
2023-505661-89-00
4
2025-12-19
Early-stage, Hormone Receptor (HR)-positive / Human Epidermal Growth F
-
2025-520979-13-00
5
2025-12-18
Patients with HR+ HER2- early breast cancer at intermediate risk of re
-
2024-518006-40-00
5
2025-11-13
Early Symptomatic Alzheimer’s Disease (MCI to Mild Dementia Due to AD)
-
2025-521775-31-00
5
2025-11-12
Stage IB-IIIA NSCLC Patients with uncommon EGFR Mutations
-
2024-512714-18-00
9
2025-11-11
Relapsing Multiple Sclerosis
-
2024-514974-39-00
5
2025-10-10
Developmental and Epileptic Encephalopathies (DEEs)
-
2024-518144-20-00
7
2025-09-03
Primary Hyperoxaluria Type 1 (PH1)
-
2024-516616-24-00
5
2025-07-23
Acromegaly
-
2024-511458-32-00
5
2025-06-15
Ulcerative colitis
-
2024-511239-91-00
4
2025-05-05
Resectable Stage I-III Non-Small Cell Lung Cancer (NSCLC)
-
2024-512536-29-00
4
2025-02-28
Amyotrophic Lateral Sclerosis (ALS)
-
2023-506537-29-00
5
2025-02-24
Haemophilia A
-
2024-513077-48-00
5
2024-12-19
O6-methylguanine methyltransferase (MGMT) unmethylated glioblastoma
-
2023-505283-11-00
6
2024-12-10
Relapsing forms of Multiple Sclerosis (RMS)
-
2023-507633-21-01
5
2024-12-09
Multiple Sclerosis
-
2023-507746-83-00
5
2024-11-27
Generalized Myasthenia Gravis
-
2024-514799-42-00
4
2024-11-05
IDIOPATHIC PULMONARY FIBROSIS
-
2023-509877-22-00
5
2024-10-30
severe von Willebrand Disease
-
2024-516433-13-00
5
2024-09-19
Progressive multiple sclerosis
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2023-509618-12-00
5
2024-09-11
Crohn's Disease (CD)