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2022-500536-11-00
5
Moderately to severely active ulcerative colitis
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2022-500537-84-00
5
Moderately to severely active ulcerative colitis
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2022-501644-15-00
4
Mild Cognitive Impairment due to Alzheimer's Disease Alzheimer's Disea
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2023-506014-47-00
9
Resected (R0 or R1) pancreatic ductal adenocarcinoma
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2023-507633-21-00
5
Neurological Disease
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2023-509861-19-00
4
Diffuse large B-cell lymphoma (DLBCL)
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2025-523766-25-00
5
Ulcerative colitis
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2023-505750-17-00
4
Neovascular age-related macular degeneration
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2023-506865-71-00
7
Relapsed/Refractory Acute Myeloid Leukemia (AML)
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2024-513445-37-00
5
previously untreated RT, irrespective of risk factors and disease stag
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2024-513579-42-00
7
Type 1 Myotonic Dystrophy
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2024-513724-42-00
10
Medulloblastoma
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2024-514682-19-00
5
Resected pancreatic ductal adenocarcinoma
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2024-517133-40-00
5
newly diagnosed, non-metastatic, SHH-activated, TP53-wt, non-MYC ampli
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2024-517269-18-00
5
stage III colon adenocarcinoma with deficient MMR
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2024-518674-14-00
5
Monogenic obesity
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2025-520631-17-00
1
Huntington’s Disease Gene Expansion Carriers
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2025-521037-86-00
5
Immune system diseases
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2025-521038-27-00
5
Immune system diseases
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2025-521113-13-00
10
Early Parkinson’s Disease
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2025-521587-35-00
5
Metastatic colorectal cancer
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2025-521908-22-00
10
EGFR-mutated Non-small Cell Lung Cancer
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2025-522145-21-00
5
Metastatic hormone sensitive prostate cancer
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2025-522343-18-00
4
Autosomal Dominant RYR1-Related Myopathy