-
2024-514173-22-00
5
2023-02-28
Cystic Fibrosis
-
2024-513545-37-00
6
2023-02-09
Polymyalgia rheumatica
-
2023-504277-20-00
5
2023-01-30
Eosinophilic esophagitis (EoE) is a rare, chronic inflammatory disorde
-
2024-511340-29-02
5
2022-12-14
Late-onset hypogonadism
-
2023-504740-33-00
5
2022-11-22
Fistulizing perianal Crohn's Disease
-
2024-515637-14-00
5
2022-11-08
Cystic Fibrosis
-
2023-505628-67-00
5
2022-10-28
Relapsed and Refractory Follicular Lymphoma
-
2023-505313-24-00
10
2022-09-30
Polycystic liver disease
-
2023-509408-13-00
6
2022-09-20
Solid tumors
-
2024-511411-25-00
5
2022-08-25
X-Linked Retinitis Pigmentosa caused by mutations in the RPGR gene
-
2023-505764-11-00
4
2022-06-10
Pruritus associated with Primary Sclerosing Cholangitis (PSC)
-
2024-514965-20-00
4
2022-06-02
Breast cancer
-
2023-507795-51-00
5
2022-05-17
atherosclerotic heart and blood vessel disease (the narrowing of arter
-
2023-504360-42-00
6
2022-05-13
Non-ST-segment elevation acute coronary syndrome
-
2023-506361-56-00
5
2022-04-01
Endometrial cancer
-
2024-515604-39-00
5
2022-01-28
Metastatic castration-resistant prostate cancer (mCRPC)
-
2023-503674-20-00
5
2021-12-17
Unresectable, locally advanced, or metastatic Non-Small Cell Lung Canc
-
2024-511492-15-00
5
2021-12-09
Duchenne Muscular Dystrophy
-
2023-506241-30-00
5
2021-11-30
Advanced Colorectal Cancer with KRAS G12C Mutation
-
2023-508248-23-00
5
2021-11-26
Non-alcoholic steatohepatitis (NASH)
-
2024-510735-21-00
5
2021-11-26
Atherosclerotic cardiovascular disease (ASCVD)
-
2023-509843-28-00
5
2021-11-10
Paroxysmal Nocturnal Hemoglobinuria (PNH)
-
2023-509380-24-00
4
2021-11-01
Metastatic upper gastrointestinal cancer, cancer of esophagus and stom
-
2023-506177-35-00
11
2021-10-23
Ovarian, fallopian tube, or primary peritoneal carcinoma.