-
2025-523013-28-00
4
2026-04-07
Endocrine-Resistant Hormone-Receptor-Positive, HER2-Negative Advanced
-
2025-522191-86-00
5
2026-04-02
Focal segmental glomerulosclerosis
-
2024-519550-36-00
6
2026-03-30
Allergic rhinoconjunctivitis
-
2024-519578-38-00
10
2026-03-30
Classic congenital adrenal hyperplasia
-
2025-521730-28-00
4
2026-03-30
Colorectal Cancer with Cancer Cachexia
-
2025-521142-22-00
5
2026-03-27
Hereditary Angioedema
-
2025-523533-25-00
10
2026-03-26
Cancer-associated Cachexia
-
2025-521884-12-00
5
2026-03-19
First line triple-negative breast cancer (TNBC)
-
2024-519555-28-00
5
2026-03-18
Dravet syndrome
-
2025-521408-24-00
5
2026-03-05
Fabry disease
-
2024-519579-24-00
5
2026-02-26
Classic Congenital Adrenal Hyperplasia
-
2025-522553-19-00
10
2026-02-25
Symptomatic genetic and familial dilated cardiomyopathy.
-
2024-519068-42-00
10
2026-02-12
Heterozygous Familial Hypercholesterolemia in pediatric patients
-
2025-522170-36-00
5
2026-02-03
Diabetes Mellitus, Type 1
-
2025-522767-15-00
5
2026-01-27
Acute Myeloid Leukemia
-
2024-512486-14-00
5
2026-01-22
Short Bowel Syndrome
-
2025-521352-38-00
5
2026-01-16
Hereditary Angioedema
-
2024-520337-80-00
5
2026-01-07
Palmoplantar Pustulosis
-
2023-509124-18-00
5
2025-12-19
Moderate-to-Severe Atopic Dermatitis
-
2024-519836-18-00
5
2025-12-16
treatment-resistant schizophrenia (TRS)
-
2025-522070-36-00
5
2025-12-15
immune thrombocytopenia (ITP)
-
2025-520461-41-00
4
2025-10-22
Systemic Sclerosis (SSc)
-
2024-519623-23-00
5
2025-10-20
Venous leg ulcer
-
2025-520582-51-00
5
2025-10-17
Hormone receptor positive breast cancer