-
2024-515059-39-00
5
2024-02-09
Marfan Syndrome
Diseases related to Marfan syndrome (rare diseases wit
-
2023-509444-10-00
7
2024-02-08
Frontotemporal Dementia With Progranulin Mutations (FTD-GRN)
-
2022-500531-36-00
4
2024-02-02
Type 1 diabetes mellitus
-
2022-502113-28-00
5
2024-02-01
Follicular lymphoma
-
2023-503327-26-00
5
2024-01-31
Sjogren's syndrome
-
2022-502980-39-00
5
2024-01-25
Estrogen receptor (ER)-positive, HER2-negative advanced breast cancer
-
2023-506971-89-00
5
2024-01-25
Coronary Artery Disease
-
2024-516607-16-00
4
2024-01-17
Neurofibromatosis type 2 is a genetically determined primary malignanc
-
2022-503092-28-00
5
2024-01-08
Relapsed/Refractory Follicular Lymphoma
-
2023-505911-19-00
4
2024-01-05
Acute Myeloid Leukemia
-
2023-504020-25-00
4
2023-12-28
Idiopathic Growth Hormone Deficiency
-
2022-502046-28-00
5
2023-12-22
HER2-Positive, PIK3CA Mutated, Locally Advanced or Metastatic Breast C
-
2022-503114-23-00
3
2023-12-19
Breast Cancer
-
2022-502159-78-00
5
2023-12-06
Chronic Spontaneous Urticaria
-
2023-503665-39-00
4
2023-11-14
Advanced cholangiocarcinoma
-
2023-503224-66-00
5
2023-10-31
Atrial Fibrillation
-
2024-517628-20-00
11
2023-10-24
hypertension
-
2023-503906-35-00
9
2023-10-11
Severe or Moderate Hemophilia A with or without factor VIII inhibitors
-
2023-510541-25-00
1
2023-10-09
Relapsed/Refractory B-cell Malignancies
-
2022-501515-14-00
5
2023-09-29
Newly Diagnosed Multiple Myeloma (NDMM)
-
2024-514441-11-00
4
2023-09-28
Ewing's sarcoma
-
2022-502281-25-00
5
2023-09-27
Focal Onset Seizures
-
2023-504973-19-01
5
2023-09-06
early-stage, intermediate-risk cervical cancer
-
2022-502732-39-00
10
2023-09-01
Previously treated non-ocular advanced melanoma