-
2022-501939-16-00
5
2023-05-09
Heart failure (HF) with mildly reduced ejection fraction (HFmrEF) or H
-
2024-510919-29-00
10
2023-05-08
Osteogenesis imperfecta (OI)
-
2022-502215-10-00
5
2023-05-04
Haemophilia A (with or without inhibitors)
-
2023-506616-41-00
5
2023-03-31
Lennox-Gastaut syndrome (LGS)
-
2023-503444-13-00
5
2023-03-29
Relapsed/refractory multiple myeloma
-
2024-512785-33-00
10
2023-03-01
Active Idiopathic Inflammatory Myopathy (IIM)
-
2024-514173-22-00
5
2023-02-28
Cystic Fibrosis
-
2024-514337-38-00
5
2023-01-24
Late-onset Ornithine transcarbamylase (OTC) deficiency
-
2023-505057-40-00
4
2022-12-02
Lung Cancer, Non-Small Cell
-
2023-504740-33-00
5
2022-11-22
Fistulizing perianal Crohn's Disease
-
2023-508284-77-00
5
2022-11-16
Generalized Myasthenia Gravis with autoantibodies against acetylcholin
-
2023-509859-13-00
5
2022-11-09
Relapsed or Refractory Multiple Myeloma (RRMM)
-
2023-508265-33-00
5
2022-10-13
Vasomotor symptoms caused by adjuvant endocrine therapy in women with,
-
2023-509229-31-00
5
2022-09-28
Metabolic Disorders - Phenylketonuria
-
2023-509750-58-00
5
2022-09-21
Polycythemia Vera
-
2023-509408-13-00
6
2022-09-20
Solid tumors
-
2023-506927-27-00
5
2022-08-29
Children with short stature either born small for gestational age or w
-
2023-507933-12-00
5
2022-08-18
Advanced or Metastatic Non-small Cell Lung Cancer (NSCLC)
-
2023-509237-39-00
5
2022-08-02
Myelin oligodendrocyte glycoprotein antibody-associated disease (MOG-A
-
2024-514891-41-00
6
2022-07-19
HR+, HER2- advanced or metastatic breast cancer
-
2023-510019-20-00
5
2022-07-13
Relapsing or refractory Eosinophilic Granulomatosis with Polyangiitis
-
2022-500014-26-00
5
2022-06-24
Locally-Advanced unresectable or Metastatic breast cancer (MBC)
-
2024-510800-35-00
5
2022-06-17
Relapsed or Refractory Multiple Myeloma (RRMM)
-
2023-503999-24-00
5
2022-06-01
Patients With Locally Advanced (Stage III), Unresectable Non-small Cel