-
2023-505640-18-00
6
2021-09-02
Spinal Muscular Atrophy
-
2023-504156-10-00
5
2021-08-13
Plaque Psoriasis.
-
2023-507146-91-00
5
2021-06-07
Duchenne Muscular Dystrophy (DMD)
-
2023-510230-84-00
5
2021-05-28
Severe asthma with an eosinophilic phenotype
-
2023-503973-39-00
5
2021-03-16
Complex Perianal Fistulas in Crohn's Disease
-
2023-507850-33-00
5
2021-02-05
Hematopoietic stem cell transplant-associated thrombotic microangiopat
-
2024-510663-34-00
4
2021-01-29
Influenza, Human
-
2024-512469-15-00
9
2020-12-08
FMS-like Tyrosine Kinase 3 (FLT3)/Internal Tandem Duplication (ITD)
Po
-
2023-506724-85-00
5
2020-11-19
Migraine
-
2023-506253-38-00
5
2020-11-09
Migraine
-
2024-514797-45-00
3
2020-08-25
Angelman Syndrome (AS)
-
2023-509935-23-00
4
2020-08-21
Duchenne Muscular Dystrophy
-
2023-503600-83-00
5
2020-05-27
Moderate to Severe Plaque Psoriasis
-
2022-501110-56-00
3
2020-02-26
Nosocomial infection, Pneumonia
-
2023-507904-30-00
3
2020-01-27
solid tumors
-
2023-506829-11-00
5
2019-05-29
Growth Hormone Deficiency in children
-
2023-503898-38-00
5
2019-05-24
Atopic Dermatitis
-
2024-510751-34-00
5
2019-03-26
Gaucher's disease type I; Gaucher's disease type III
-
2022-502936-38-00
5
2019-01-09
Moderate and Severe Atopic Dermatitis
-
2023-508955-37-00
5
2018-10-10
Moderate to severe atopic dermatitis
-
2023-509440-97-00
3
2018-09-25
Relapsed/Refractory B-precursor Acute Lymphoblastic Leukemia (r/r ALL)
-
2024-515835-31-00
7
2018-03-20
Mucopolysaccharidosis type IIIA (Sanfilippo A syndrome)
-
2024-514698-23-00
5
2017-05-15
Patients with Duchenne Muscular Dystrophy Amenable to Exon 45 or 53 Sk
-
2024-512730-15-00
4
2012-09-14
Systemic Lupus Erythematosus