Metachromatic leukodystrophy

5 total trials MedDRA PT

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A clinical trial to evaluate the effect of OTL-200, a gene therapy treatment in patients with Late Juvenile (LJ) Metachromatic Leukodystroph … Recruitment ended

2024-511971-13-00 5 2020-09-11 "Metachromatic Leukodystrophy (MLD) is an autosomal recessive"
A Single-arm Study of Intrathecal SHP611 in Subjects with Metachromatic Leukodystrophy Ended

2024-514402-31-00 4 2019-09-09 "Late Metachromatic Leukodystrophy (MLD)"
Gene therapy study using a frozen formulation of OTL-200 in patients with Metachromatic Leukodystrophy (MLD) Ended

2024-511970-66-00 5 2017-12-13 "Metachromatic Leukodystrophy (MLD)"
A safety and efficacy extension of study HGT-MLD-070 in Children with Metachromatic Leukodystrophy recieving enzyme (HGT-1110) replacement b … Ended

2024-514403-34-00 9 2012-10-10 "Late Metachromatic Leukodystrophy (MLD)"
Hematopoietic stem cell gene therapy study Ended

2024-515253-25-00 9 2010-04-08 "Metachromatic Leukodystrophy (MLD)"

Showing 1–5 of 5 trials