Adeno-Associated Viral Vector Serotype 9 Expressing Codon-Optimized Human Gba Gene

2 trials Orphan designation

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2 Registered trials
0 Recruiting
0 Completed trials
1 Sponsors
3 Countries
Phase I/II: 1 Phase I (FiH): 1
Oversight events:
4 temporary halts across 1 trial
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Indications tested

Gaucher's disease type I 1

Sponsors using this IMP

Prevail Therapeutics Inc. 2

All trials

2 total

Showing 1–2 of 2 trials

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