Alagille syndrome

2 trials 1 recruiting MedDRA PT
2 Registered trials
1 Recruiting
2 Unique sponsors
2 Unique IMPs
2 Commercial trials
Drug classes (ATC)
A Gastroenterology (ATC A) 2
Mechanism of action (INN-stem analysis)
Unknown / small molecule 2 substances
Phase III: 1 Phase IV: 1

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Show: 2 trials

Phase III

1 trial

Phase IV

1 trial
  • Mirum Pharmaceuticals Inc. Commercial
    MARALIXIBAT
    2024-516804-40-00 6 countries 2025 n=223 Orphan
    Recruiting
Sponsor activity
SponsorTypeTrialsPhasesRecruiting
Ipsen Pharma Commercial 1 Phase III 0
Mirum Pharmaceuticals Inc. Commercial 1 Phase IV 1
New trials by year
2022
1
2025
1
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