Amyotrophic lateral sclerosis gene carrier

1 trials MedDRA PT
1 Registered trials
0 Recruiting
1 Unique sponsors
1 Unique IMPs
1 Commercial trials
Drug classes (ATC)
ATC code not specified 1
Mechanism of action (INN-stem analysis)
Antisense oligonucleotide 1 substance
Phase III: 1

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Phase III

1 trial
  • Biogen Idec Research Limited Commercial
    TOFERSEN
    2023-505641-12-00 6 countries 2021 n=30 Orphan
    Ended
Sponsor activity
SponsorTypeTrialsPhasesRecruiting
Biogen Idec Research Limited Commercial 1 Phase III 0
New trials by year
2021
1
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