Congenital myopathy

3 trials MedDRA PT
3 Registered trials
0 Recruiting
3 Unique sponsors
3 Unique IMPs
2 Commercial trials
Drug classes (ATC)
ATC code not specified 2
R Respiratory (ATC R) 2
Mechanism of action (INN-stem analysis)
Unknown / small molecule 3 substances
Phase II: 1 Phase IV: 2 Phase I (First in Human): 1

Filter these 3 trials by country, sponsor, date range and more.

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Show: 3 trials

Phase II

1 trial
  • Rycarma Therapeutics Inc. Commercial
    SURLORIAN
    2025-522343-18-00 4 countries n=41
    Pending

Phase IV

2 trials
  • Vaestra Goetalandsregionen Academic
    SALBUTAMOL
    2024-512027-36-00 1 country 2021 n=20
    Ended
  • Vaestra Goetalandsregionen Academic
    SALBUTAMOL
    2024-512027-36-00 1 country 2021 n=20
    Ended

Phase I (First in Human)

1 trial
  • Astellas Gene Therapies Inc. Commercial
    ASP2957
    2025-523213-29-00 1 country n=3
    Pending
Sponsor activity
SponsorTypeTrialsPhasesRecruiting
Vaestra Goetalandsregionen Academic 2 Phase IV 0
Rycarma Therapeutics Inc. Commercial 1 Phase II 0
Astellas Gene Therapies Inc. Commercial 1 Phase I (First in Human) 0
New trials by year
2021
2
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