Familial dilated cardiomyopathy

1 trials 1 recruiting MedDRA PT
1 Registered trials
1 Recruiting
1 Unique sponsors
4 Unique IMPs
1 Commercial trials
Drug classes (ATC)
H Endocrinology (ATC H) 1
J Anti-infectives (ATC J) 1
L Oncology (ATC L) 1
Mechanism of action (INN-stem analysis)
Unknown / small molecule 2 substances
Corticosteroid 1 substance
mTOR inhibitor 1 substance
Phase I (First in Human): 1

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Show: 1 trials

Phase I (First in Human)

1 trial
  • Alexion Pharmaceuticals Inc. Commercial
    AAV9-CTNT-COBAG3; PREDNISONE; SIROLIMUS; SULFAMETHOXAZOLE, TRIMETHOPRIM
    2024-519674-40-00 3 countries 2026 n=8
    Recruiting
Sponsor activity
SponsorTypeTrialsPhasesRecruiting
Alexion Pharmaceuticals Inc. Commercial 1 Phase I (First in Human) 1
New trials by year
2026
1
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