Glycogen storage disease type I

1 trials MedDRA PT
1 Registered trials
0 Recruiting
1 Unique sponsors
2 Unique IMPs
1 Commercial trials
Drug classes (ATC)
B Haematology (ATC B) 1
Mechanism of action (INN-stem analysis)
Unknown / small molecule 1 substance
Supportive / diluent 1 substance
Phase I (First in Human): 1

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Phase I (First in Human)

1 trial
  • Moderna Inc. Commercial
    MRNA ENCODING HUMAN GLUCOSE-6-PHOSPHATASE VARIANT S298C; SODIUM CHLORIDE
    2022-502963-39-00 4 countries 2024 n=24 Orphan
    Ended
Sponsor activity
SponsorTypeTrialsPhasesRecruiting
Moderna Inc. Commercial 1 Phase I (First in Human) 0
New trials by year
2024
1
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