Hereditary optic atrophy

2 trials 1 recruiting MedDRA PT
2 Registered trials
1 Recruiting
2 Unique sponsors
2 Unique IMPs
1 Commercial trials
Drug classes (ATC)
— ATC code not specified 1
A Gastroenterology (ATC A) 1
Mechanism of action (INN-stem analysis)
Unknown / small molecule 2 substances
Phase II: 1 Phase I: 1

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Show: 2 trials

Phase II

1 trial
  • Centre Hospitalier Universitaire D'Angers Academic
    NICOTINAMIDE
    2025-524343-13-00 1 country n=13
    Pending

Phase I

1 trial
  • Stoke Therapeutics Inc. Commercial
    18‐MER ANTISENSE OLIGONUCLEOTIDE COMPLEMENTARY TO OPA1 PRE-MRNA
    2023-506290-35-00 4 countries 2025 n=35
    Recruiting
Sponsor activity
SponsorTypeTrialsPhasesRecruiting
Stoke Therapeutics Inc. Commercial 1 Phase I 1
Centre Hospitalier Universitaire D'Angers Academic 1 Phase II 0
New trials by year
2025
1
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