Homocystinuria

1 trials MedDRA PT
1 Registered trials
0 Recruiting
1 Unique sponsors
1 Unique IMPs
1 Commercial trials
Drug classes (ATC)
N Neurology/Psychiatry (ATC N) 1
Mechanism of action (INN-stem analysis)
Unknown / small molecule 1 substance
Phase III: 1

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Phase III

1 trial
  • Travere Therapeutics Inc. Commercial
    PEGTIBATINASE
    2023-504135-40-00 8 countries n=22 Orphan
    Pending
Sponsor activity
SponsorTypeTrialsPhasesRecruiting
Travere Therapeutics Inc. Commercial 1 Phase III 0
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