5
Registered trials
3
Recruiting
2
Unique sponsors
2
Unique IMPs
5
Commercial trials
Drug classes (ATC)
—
ATC code not specified
2
M
Musculoskeletal (ATC M)
3
Mechanism of action (INN-stem analysis)
Kinase inhibitor
1 substance
Unknown / small molecule
1 substance
Phase III:
2
Phase II/III:
1
Phase II:
2
Phase III
2 trials-
EndedBiomarin Pharmaceutical Inc. CommercialVOSORITIDE
-
RecruitingBiomarin Pharmaceutical Inc. CommercialVOSORITIDE
Phase II/III
1 trial-
RecruitingQed Therapeutics Inc. CommercialINFIGRATINIB
Phase II
2 trials-
RecruitingBiomarin Pharmaceutical Inc. CommercialVOSORITIDE
-
PendingQed Therapeutics Inc. CommercialINFIGRATINIB
Sponsor activity
| Sponsor | Type | Trials | Phases | Recruiting |
|---|---|---|---|---|
| Biomarin Pharmaceutical Inc. | Commercial | 3 | Phase II, Phase III | 2 |
| Qed Therapeutics Inc. | Commercial | 2 | Phase II/III, Phase II | 1 |
New trials by year
2024
1
2025
2
2026
1