Methylmalonic aciduria

1 trials 1 recruiting MedDRA PT
1 Registered trials
1 Recruiting
1 Unique sponsors
1 Unique IMPs
1 Commercial trials
Drug classes (ATC)
ATC code not specified 1
Mechanism of action (INN-stem analysis)
Unknown / small molecule 1 substance
Phase I (First in Human): 1

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Phase I (First in Human)

1 trial
  • Moderna Inc. Commercial
    MODIFIED MRNA ENCODING HUMAN METHYLMALONYL-COENZYME A MUTASE CONTAINING A POLYMORPHISM AT POSITION 671
    2022-501997-20-00 3 countries 2023 n=26 Orphan
    Recruiting
Sponsor activity
SponsorTypeTrialsPhasesRecruiting
Moderna Inc. Commercial 1 Phase I (First in Human) 1
New trials by year
2023
1
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