Mucopolysaccharidosis II

2 trials 1 recruiting MedDRA PT
2 Registered trials
1 Recruiting
1 Unique sponsors
2 Unique IMPs
2 Commercial trials
Drug classes (ATC)
— ATC code not specified 1
A Gastroenterology (ATC A) 1
Mechanism of action (INN-stem analysis)
Unknown / small molecule 2 substances
Phase III: 2

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Show: 2 trials

Phase III

2 trials
  • Jcr Pharmaceuticals Co. Ltd. Commercial
    PABINAFUSP ALFA
    2022-503142-41-00 5 countries 2024 n=32 Orphan
    Recruiting
  • Jcr Pharmaceuticals Co. Ltd. Commercial
    IDURSULFASE; PABINAFUSP ALFA
    2024-512289-33-00 5 countries 2022 n=35 Orphan
    Ended
Sponsor activity
SponsorTypeTrialsPhasesRecruiting
Jcr Pharmaceuticals Co. Ltd. Commercial 2 Phase III 1
New trials by year
2022
1
2024
1
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