Niemann-Pick disease

3 trials MedDRA PT
3 Registered trials
0 Recruiting
3 Unique sponsors
3 Unique IMPs
1 Commercial trials
Drug classes (ATC)
— ATC code not specified 2
A Gastroenterology (ATC A) 1
Mechanism of action (INN-stem analysis)
Unknown / small molecule 3 substances
Phase III: 1 Phase II: 2

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Show: 3 trials

Phase III

1 trial
  • Cyclo Therapeutics Inc. Academic
    HYDROXYPROPYLBETADEX; MIGLUSTAT
    2024-518266-27-00 4 countries 2022 n=36 Orphan
    Ended

Phase II

2 trials
  • Sanofi Winthrop Industrie Commercial
    OLIPUDASE ALFA
    2024-515304-39-00 1 country 2021 n=3 Orphan
    Ended
  • Bellvitge University Hospital Academic
    IMP not specified
    2023-505832-36-01 1 country 2024 n=16
    Ended
Sponsor activity
SponsorTypeTrialsPhasesRecruiting
Sanofi Winthrop Industrie Commercial 1 Phase II 0
Bellvitge University Hospital Academic 1 Phase II 0
Cyclo Therapeutics Inc. Academic 1 Phase III 0
New trials by year
2021
1
2022
1
2024
1
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