Noonan syndrome

2 trials 1 recruiting MedDRA PT
2 Registered trials
1 Recruiting
2 Unique sponsors
2 Unique IMPs
2 Commercial trials
Drug classes (ATC)
M Musculoskeletal (ATC M) 1
N Neurology/Psychiatry (ATC N) 1
ATC code not specified 1
Mechanism of action (INN-stem analysis)
Unknown / small molecule 2 substances
Phase III: 1 Phase II: 1

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Show: 2 trials

Phase III

1 trial
  • Novo Nordisk A/S Commercial
    SOMAPACITAN
    2022-501055-87-01 3 countries 2023 n=20 Orphan
    Ended

Phase II

1 trial
  • Biomarin Pharmaceutical Inc. Commercial
    VOSORITIDE
    2024-515861-33-00 4 countries 2025 n=40 Orphan
    Recruiting
Sponsor activity
SponsorTypeTrialsPhasesRecruiting
Biomarin Pharmaceutical Inc. Commercial 1 Phase II 1
Novo Nordisk A/S Commercial 1 Phase III 0
New trials by year
2023
1
2025
1
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