3
Registered trials
2
Recruiting
3
Unique sponsors
3
Unique IMPs
3
Commercial trials
Drug classes (ATC)
—
ATC code not specified
1
N
Neurology/Psychiatry (ATC N)
2
Mechanism of action (INN-stem analysis)
Unknown / small molecule
2 substances
siRNA
1 substance
Phase III:
1
Phase II:
1
Phase I (First in Human):
1
Phase III
1 trial-
PendingBiocodex CommercialSTIRIPENTOL
Phase II
1 trial-
RecruitingDicerna Pharmaceuticals Inc. CommercialNEDOSIRAN
Phase I (First in Human)
1 trial-
RecruitingArbor Biotechnologies Inc. CommercialMRNA-002, GRNA-001
Sponsor activity
| Sponsor | Type | Trials | Phases | Recruiting |
|---|---|---|---|---|
| Dicerna Pharmaceuticals Inc. | Commercial | 1 | Phase II | 1 |
| Biocodex | Commercial | 1 | Phase III | 0 |
| Arbor Biotechnologies Inc. | Commercial | 1 | Phase I (First in Human) | 1 |
New trials by year
2021
1
2025
1