Pseudoxanthoma elasticum

2 trials 1 recruiting MedDRA PT
2 Registered trials
1 Recruiting
2 Unique sponsors
2 Unique IMPs
1 Commercial trials
Drug classes (ATC)
ATC code not specified 2
Mechanism of action (INN-stem analysis)
Unknown / small molecule 2 substances
Phase III: 1 Phase II: 1

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Show: 2 trials

Phase III

1 trial
  • Universitair Medisch Centrum Utrecht Academic
    ETIDRONATE DISODIUM
    2024-512133-33-00 1 country 2023 n=76
    Ended

Phase II

1 trial
  • Inozyme Pharma Inc. Commercial
    RECOMBINANT HUMAN ECTONUCLEOTIDE PYROPHOSPHATASE/PHOSPHODIESTERASE 1 FUSED TO THE FC FRAGMENT OF IGG1
    2024-512715-42-00 2 countries 2024 n=14 Orphan
    Recruiting
Sponsor activity
SponsorTypeTrialsPhasesRecruiting
Inozyme Pharma Inc. Commercial 1 Phase II 1
Universitair Medisch Centrum Utrecht Academic 1 Phase III 0
New trials by year
2023
1
2024
1
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