Rett syndrome

2 trials MedDRA PT
2 Registered trials
0 Recruiting
2 Unique sponsors
2 Unique IMPs
2 Commercial trials
Drug classes (ATC)
ATC code not specified 1
N Neurology/Psychiatry (ATC N) 1
Mechanism of action (INN-stem analysis)
Unknown / small molecule 2 substances
Phase III: 1 Phase II: 1

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Show: 2 trials

Phase III

1 trial
  • UCB Biosciences Inc. Commercial
    FENFLURAMINE HYDROCHLORIDE
    2025-523157-34-00 7 countries n=82 Orphan
    Pending

Phase II

1 trial
  • Minoryx Therapeutics S.L. Commercial
    LERIGLITAZONE
    2024-514684-26-00 1 country 2024 n=24 Orphan
    Ended
Sponsor activity
SponsorTypeTrialsPhasesRecruiting
Minoryx Therapeutics S.L. Commercial 1 Phase II 0
UCB Biosciences Inc. Commercial 1 Phase III 0
New trials by year
2024
1
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