Short stature homeobox gene mutation

1 trials 1 recruiting MedDRA PT
1 Registered trials
1 Recruiting
1 Unique sponsors
1 Unique IMPs
1 Commercial trials
Drug classes (ATC)
M Musculoskeletal (ATC M) 1
N Neurology/Psychiatry (ATC N) 1
Mechanism of action (INN-stem analysis)
Unknown / small molecule 1 substance
Phase II: 1

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Phase II

1 trial
  • Biomarin Pharmaceutical Inc. Commercial
    VOSORITIDE
    2024-515861-33-00 4 countries 2025 n=40 Orphan
    Recruiting
Sponsor activity
SponsorTypeTrialsPhasesRecruiting
Biomarin Pharmaceutical Inc. Commercial 1 Phase II 1
New trials by year
2025
1
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