Clinical study to evaluate the safety and tolerability of SPVN06 (novel gene therapy) in a subset of patients with rod cone dystrophy (RCD).

2022-501250-12-01 Protocol SPVN06-CLIN-01 Phase I and Phase II (Integrated) - First administration to humans Ongoing, recruitment ended

Start 17 Mar 2023 · Status Ongoing, recruitment ended · 1 EU/EEA countries · 1 sites · Protocol SPVN06-CLIN-01

Overview

Sponsor-declared trial summary

Phase Phase I and Phase II (Integrated) - First administration to humans
Status Ongoing, recruitment ended
Participants planned 33
Countries 1
Sites 1

Inherited retinal dystrophies

Key facts

Sponsor
Sparingvision
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Eye Diseases [C11]
Trial duration
17 Mar 2023 → ongoing
Decision date (initial)
2023-03-03
Transition trial
No
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
No

External identifiers

EU CT number
2022-501250-12-01
ClinicalTrials.gov
NCT05748873

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Inherited retinal dystrophies

VersionLevelCodeTermSystem organ class
20.0 PT 10019899 Hereditary retinal dystrophy 100000004850

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Sparingvision

Sponsor organisation
Sparingvision
Address
5 Avenue Percier
City
Paris
Postcode
75008
Country
France

Scientific contact point

Organisation
Sparingvision
Contact name
Daniel Chung

Public contact point

Organisation
Sparingvision
Contact name
Sophie Skorupka

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
France Ongoing, recruitment ended 17 1
Rest of world
United States
16

Investigational sites

France

1 site · Ongoing, recruitment ended
Quinze-Vingts National Ophthalmology Hospital
Electrophysiology unit, 28 Rue De Charenton, 75012, Paris

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
France 2023-03-17 2023-04-12 2026-03-04

Application history

11 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2022-12-16 France Acceptable
2023-02-17
2023-03-03
2 SUBSTANTIAL MODIFICATION SM-1 2023-07-25 France Acceptable
2023-09-22
2023-09-25
3 NON SUBSTANTIAL MODIFICATION NSM-1 2023-09-27 France 2023-09-27
4 SUBSTANTIAL MODIFICATION SM-2 2023-12-14 France Acceptable
2024-01-08
2024-01-30
5 NON SUBSTANTIAL MODIFICATION NSM-3 2024-02-12 France Acceptable
2024-01-08
2024-02-12
6 SUBSTANTIAL MODIFICATION SM-4 2024-03-07 France Acceptable
2024-04-23
2024-04-23
7 NON SUBSTANTIAL MODIFICATION NSM-4 2024-05-31 France Acceptable
2024-04-23
2024-05-31
8 SUBSTANTIAL MODIFICATION SM-5 2025-01-14 France Acceptable
2025-03-13
2025-03-13
9 SUBSTANTIAL MODIFICATION SM-6 2025-06-25 France Acceptable
2025-08-26
2025-08-28
10 SUBSTANTIAL MODIFICATION SM-7 2025-10-10 France Acceptable
2025-11-06
2025-11-07
11 NON SUBSTANTIAL MODIFICATION NSM-6 2026-02-11 France Acceptable
2025-11-06
2026-02-11