Study of safety, tolerability and efficacy of DFV890 in adult participants with myeloid diseases

2022-501406-36-00 Protocol CDFV890G12101 Human pharmacology (Phase I) - Other Ongoing, recruitment ended

Start 14 Dec 2023 · Status Ongoing, recruitment ended · 4 EU/EEA countries · 12 sites · Protocol CDFV890G12101

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - Other
Status Ongoing, recruitment ended
Participants planned 94
Countries 4
Sites 12

Myeloid disease

Key facts

Sponsor
Novartis Pharma AG
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Neoplasms [C04]
Trial duration
14 Dec 2023 → ongoing
Decision date (initial)
2023-03-29
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
Yes

External identifiers

EU CT number
2022-501406-36-00
ClinicalTrials.gov
NCT05552469

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Myeloid disease

VersionLevelCodeTermSystem organ class
21.0 LLT 10028548 Myeloid dysplasia 10029104

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Novartis Pharma AG

Sponsor organisation
Novartis Pharma AG
Address
Lichtstrasse 35
City
Basel Town
Postcode
4056
Country
Switzerland

Scientific contact point

Organisation
Novartis Pharma AG
Contact name
Novartis Pharma Arzneimittel GmbH

Public contact point

Organisation
Novartis Pharma AG
Contact name
Novartis Pharma Arzneimittel GmbH

Locations

4 EU/EEA countries · 12 investigational sites

By country

CountryMS statusPlanned subjectsSites
France Ongoing, recruitment ended 8 4
Germany Ongoing, recruitment ended 9 4
Italy Ended 12 2
Spain Ongoing, recruitment ended 10 2
Rest of world
United States, Hong Kong, United Kingdom, Singapore
55

Investigational sites

France

4 sites · Ongoing, recruitment ended
Centre Hospitalier Universitaire Grenoble Alpes
6001: Hematology, Boulevard De La Chantourne, Cs 10217 La Tronche, Grenoble Cedex 9
Centre Hospitalier Universitaire De Nantes
6000: Hematology, 1 Place Alexis Ricordeau, 44000, Nantes
Hopital Saint Louis
6002:Hematology, 1 Avenue Claude Vellefaux, 75010, Paris
Institut Paoli Calmettes
6003:Hematology, 232 Boulevard De Sainte Marguerite, Bp 156, Marseille

Germany

4 sites · Ongoing, recruitment ended
Universitaetsklinikum Schleswig-Holstein AöR
9004:Klinik Haematologie und Onkologie Campus Luebeck, Ratzeburger Allee 160, 23538, Luebeck
Universitaetsklinikum Duesseldorf AöR
9003:Klinik für Hämatologie, Onkologie und klinische Immunologie, Moorenstrasse 5, Bilk, Duesseldorf
University of Leipzig
9000: Medical Department for Haematology, Cell Therapy and Hemostaseology, Liebigstrasse 22, Zentrum-Suedost, Leipzig
Technische Universitat Dresden
9001: Medizinische Klinik und Poliklinik I, Fetscherstrasse 74, Johannstadt-Nord, Dresden

Italy

2 sites · Ended
Azienda Socio Sanitaria Territoriale Degli Spedali Civili Di Brescia
7001:UO Ematologia, Piazzale Spedali Civili 1, 25123, Brescia
Humanitas Research Hospital
7000: U.O. Ematologia, Via Alessandro Manzoni 56, 20089, Rozzano

Spain

2 sites · Ongoing, recruitment ended
Hospital Universitario 12 De Octubre
8002 Hematology, Bloque D, Avenida De Cordoba S/n, Madrid
Hospital Universitario Ramon Y Cajal
8001 Hematology, Carretera Del Colmenar Viejo Km 9 100, Por El Pardo, Madrid

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
France 2024-03-12 2024-03-12 2025-12-19
Germany 2024-01-18 2024-01-18 2025-12-02
Italy 2023-12-14 2023-12-14 2024-03-26
Spain 2023-12-29 2023-12-29 2025-11-04

Application history

8 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2022-11-23 Germany Acceptable
2023-03-27
2023-03-29
2 SUBSTANTIAL MODIFICATION SM-1 2023-08-16 Germany Acceptable
2023-11-03
2023-11-07
3 SUBSTANTIAL MODIFICATION SM-2 2024-01-12 Germany Acceptable
2024-02-26
2024-02-28
4 SUBSTANTIAL MODIFICATION SM-3 2024-10-11 Germany Acceptable 2024-11-26
5 NON SUBSTANTIAL MODIFICATION NSM-1 2024-12-13 Germany Acceptable 2024-12-13
6 SUBSTANTIAL MODIFICATION SM-4 2025-01-22 Germany Acceptable
2025-03-18
2025-03-18
7 SUBSTANTIAL MODIFICATION SM-5 2025-05-14 Germany Acceptable
2025-07-23
2025-07-23
8 SUBSTANTIAL MODIFICATION SM-6 2025-09-26 Germany Acceptable 2025-10-21