Semaglutide Treatment for Prevention of Toxicity in High-dose Chemotherapy with Autologous Hematopoietic Stem Cell Transplantation

2022-502139-20-00 Protocol PROTECT Therapeutic exploratory (Phase II) Ongoing, recruiting

Start 9 Sep 2024 · Status Ongoing, recruiting · 1 EU/EEA countries · 2 sites · Protocol PROTECT

Overview

Sponsor-declared trial summary

Phase Therapeutic exploratory (Phase II)
Status Ongoing, recruiting
Participants planned 40
Countries 1
Sites 2

Mucositis and systemical inflammation, which is a treatment-related complication after treatment with high-dose chemotherapy

To evaluate the effect of semaglutide in reducing intensity of gastrointestinal (GI) mucositis in patients undergoing high-dosage chemotherapy followed by autologous (auto) hematopoietic stem cell transplantation (HSCT).

Key facts

Sponsor
Rigshospitalet
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Digestive System Diseases [C06]
Trial duration
9 Sep 2024 → ongoing
Decision date (initial)
2023-03-21
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
No

External identifiers

EU CT number
2022-502139-20-00
WHO UTN
U1111-1277-7868

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Therapy, Safety, Prophylaxis

To evaluate the effect of semaglutide in reducing intensity of gastrointestinal (GI) mucositis in patients undergoing high-dosage chemotherapy followed by autologous (auto) hematopoietic stem cell transplantation (HSCT).

Secondary objectives 1

  1. To evaluate the effect and safety of semaglutide in reducing gut barrier injury and systemic inflammation in patients undergoing auto-HSCT.

Conditions and MedDRA coding

Mucositis and systemical inflammation, which is a treatment-related complication after treatment with high-dose chemotherapy

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 5

  1. Referral for auto-HSCT for relapsed diffuse large B-cell lymphoma (DLBCL) or follicular lymphoma
  2. Age ≥ 18 years
  3. BMI ≥ 18.5
  4. ECOG performance status ≤ 2
  5. Literate in Danish and/or English

Exclusion criteria 10

  1. Diabetes
  2. Previous or current gastrointestinal malignancy
  3. Personal or family history of medullary thyroid carcinoma or multiple endocrine neoplasia syndrome type 2. Family is defined as a first degree relative
  4. Genetic disorders with defective tissue repair (e.g. Fanconi anaemia)
  5. History of pancreatitis (acute or chronic)
  6. Renal impairment measured as estimated Glomerular Filtration Rate (eGFR) value of < 30 ml/min/1.73 m2 as defined by KDIGO 2012 classification4
  7. Impaired liver function, defined as ALT ≥ 2.5 times upper normal limit at screening
  8. Known or suspected hypersensitivity to semaglutide or other GLP-1RA
  9. Inflammatory bowel disease
  10. Pregnant or nursing females

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. GI mucositis severity: mean severity grade (0-II) from study week 5 to 9

Secondary endpoints 3

  1. CRP increment in the early post-transplant phase: area under the plasma concentration-time curve (AUC) from study week 5 to 8
  2. Quality of life (QOL): change from baseline (study week 4) to study week 9 and 18 evaluated by EORTC QLQ-C30 and EORTC QLQ-HDC29 questionnaires
  3. Safety profile: evaluated by SAR according to ICH-GCP guidelines

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 1

Ozempic 0.25 mg solution for injection in pre-filled pen

PRD6392561 · Product

Active substance
Semaglutide
Pharmaceutical form
SOLUTION FOR INJECTION
Route of administration
SUBCUTANEOUS INJECTION
Max daily dose
0.5 mg milligram(s)
Max total dose
4 mg milligram(s)
Max treatment duration
12 Week(s)
Authorisation status
Authorised
ATC code
A10BJ06 — -
Marketing authorisation
EU/1/17/1251/002
MA holder
NOVO NORDISK A/S
MA country
EU
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Placebo 1

Semaglutide placebo (saline), Pharmaceutical form: Solution for injection, Route of administration: Subcutaneous injection, 1.5 ml pre-filled pen-injector

N/A · Product

Other product name
N/A
Pharmaceutical form
N/A
ATC code
N/A — N/A
Marketing authorisation
N/A
MA holder
N/A
MA country
Iceland
Paediatric formulation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Rigshospitalet

Sponsor organisation
Rigshospitalet
Address
Blegdamsvej 9
City
Copenhagen Oe
Postcode
2100
Country
Denmark

Scientific contact point

Organisation
Rigshospitalet
Contact name
Klaus Müller

Public contact point

Organisation
Rigshospitalet
Contact name
Klaus Müller

Third parties 1

OrganisationCity, countryDuties
University Of Copenhagen
ORG-100030460
Frederiksberg C, Denmark On site monitoring

Locations

1 EU/EEA country · 2 investigational sites

By country

CountryMS statusPlanned subjectsSites
Denmark Ongoing, recruiting 40 2
Rest of world 0

Investigational sites

Denmark

2 sites · Ongoing, recruiting
Rigshospitalet
Department of Haematology, Blegdamsvej 9, 2100, Copenhagen Oe
Zealand University Hospital
Department of Haematology, Sygehusvej 10, 4000, Roskilde

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Denmark 2024-09-09 2024-09-11

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 3 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) Study Protocol_PROTECT 3
Summary of Product Characteristics (SmPC) (for publication) ozempic-epar-product-information_en 1
Synopsis of the protocol (for publication) Protocol summary_PROTECTv2 1

Application history

3 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2022-11-22 Denmark Acceptable
2023-02-22
2023-03-21
2 NON SUBSTANTIAL MODIFICATION NSM-1 2025-05-19 Denmark Acceptable
2023-02-22
2025-05-19
3 SUBSTANTIAL MODIFICATION SM-2 2025-06-02 Denmark Acceptable
2025-06-18
2025-06-18