Hyperpolarized 129-Xenon MRI in Fibrosing Interstitial Lung Disease

2022-502512-36-00 Protocol Xe-F-ILD-001 Therapeutic exploratory (Phase II) Ongoing, recruitment ended

Start 2 Oct 2023 · Status Ongoing, recruitment ended · 1 EU/EEA countries · 2 sites · Protocol Xe-F-ILD-001

Overview

Sponsor-declared trial summary

Phase Therapeutic exploratory (Phase II)
Status Ongoing, recruitment ended
Participants planned 39
Countries 1
Sites 2

Progressive Fibrosing Interstitial Lung Diseases

This project aims to investigate the potential of non-invasive imaging to identify and monitor the earliest signs and physiological effects of pulmonary fibrosis and resulting cardiac dysfunction in patients with fibrosing interstitial lung disease. Second, to evaluate baseline risk factors the progression and therapeu…

Key facts

Sponsor
Aarhus University
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Respiratory Tract Diseases [C08], Analytical, Diagnostic and Therapeutic Techniques and Equipment [E] - Investigative Techniques [E05]
Trial duration
2 Oct 2023 → ongoing
Decision date (initial)
2023-03-06
Transition trial
No
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
No
Funding sources
Karen Elise Jensens Fond · Aarhus University

External identifiers

EU CT number
2022-502512-36-00
WHO UTN
U1111-1284-7436
ClinicalTrials.gov
NCT05914506

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Efficacy, Diagnosis

This project aims to investigate the potential of non-invasive imaging to identify and monitor the earliest signs and physiological effects of pulmonary fibrosis and resulting cardiac dysfunction in patients with fibrosing interstitial lung disease. Second, to evaluate baseline risk factors the progression and therapeutic responses to anti-fibrotic drugs.

Conditions and MedDRA coding

Progressive Fibrosing Interstitial Lung Diseases

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 4

  1. Patients diagnosed with IPF or fibrotic ILD who fulfills PPF criteria, and are prescribed antifibrotic treatment.
  2. Age 18-90
  3. Cognitively able to understand and participate in the study
  4. Pre-menopausal women must be confirmed non-pregnant by an onsite test.

Exclusion criteria 7

  1. Contraindications for MRI (Pacemaker, neurostimulator or cochlear implant; Metal foreign bodies such as fragments and irremovable piercings; Unsafe medical implants (safety of heart valves, hips and the like must be confirmed); Intrathoracic clips or coils; Cardiac pacemakers; Claustrophobia; Largest circumference including arms > 160 cm)
  2. Contraindications to gadolinium contrast (eGFR < 30 mL/min/1.73m2; Previous adverse reactions to gadolinium)
  3. Overlapping emphysematic disease where the emphysema-component outweighs the fibrosis
  4. Unable to perform breath-hold of minimum 20 seconds.
  5. Allergy to Xenon
  6. Breast feeding
  7. Evidence of ongoing respiratory infections at time of MR examinations

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 4

  1. MR xenon ventilation and dissolved parameters
  2. Worsening of pulmonary function test parameters
  3. Worsening of HRCT parameters
  4. Worsening in patient reported symptoms

Secondary endpoints 3

  1. Regionally decreased perfusion
  2. Evidence of myocardial stran and fibrosis
  3. Late contrast enhancement

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 5

Hyperpolarised 129Xe 500 ml

PRD10485548 · Product

Active substance
Xenon (129XE)
Pharmaceutical form
INHALATION SOLUTION
Route of administration
INHALATION
Max daily dose
12 l litre(s)
Max total dose
12 l litre(s)
Max treatment duration
2 Day(s)
Authorisation status
Not Authorised
MA holder
AARHUS UNIVERSITY
Paediatric formulation
No
Orphan designation
No

Hyperpolarised 129Xe 650 ml

PRD10485529 · Product

Active substance
Xenon (129XE)
Pharmaceutical form
INHALATION SOLUTION
Route of administration
INHALATION
Max daily dose
12 l litre(s)
Max total dose
12 l litre(s)
Max treatment duration
2 Day(s)
Authorisation status
Not Authorised
MA holder
AARHUS UNIVERSITY
Paediatric formulation
No
Orphan designation
No

Hyperpolarised 129Xe 400 ml

PRD10485562 · Product

Active substance
Xenon (129XE)
Pharmaceutical form
INHALATION SOLUTION
Route of administration
INHALATION
Max daily dose
12 l litre(s)
Max total dose
12 l litre(s)
Max treatment duration
2 Day(s)
Authorisation status
Not Authorised
MA holder
AARHUS UNIVERSITY
Paediatric formulation
No
Orphan designation
No

Hyperpolarised 129Xe gas 1000 ml

PRD10485456 · Product

Active substance
Xenon (129XE)
Pharmaceutical form
INHALATION SOLUTION
Route of administration
INHALATION
Max daily dose
12 l litre(s)
Max total dose
12 l litre(s)
Max treatment duration
2 Day(s)
Authorisation status
Not Authorised
MA holder
AARHUS UNIVERSITY
Paediatric formulation
No
Orphan designation
No

Hyperpolarised 129Xe 800 ml

PRD10485510 · Product

Active substance
Xenon (129XE)
Pharmaceutical form
INHALATION SOLUTION
Route of administration
INHALATION
Max daily dose
12 l litre(s)
Max total dose
12 l litre(s)
Max treatment duration
2 Day(s)
Authorisation status
Not Authorised
MA holder
AARHUS UNIVERSITY
Paediatric formulation
No
Orphan designation
No

Auxiliary 1

Gadovist, injektionsvæske, opløsning

PRD385362 · Product

Active substance
Gadobutrol
Pharmaceutical form
SOLUTION FOR INJECTION
Route of administration
INJECTION
Max daily dose
20 ml millilitre(s)
Max total dose
40 ml millilitre(s)
Max treatment duration
2 Day(s)
Authorisation status
Authorised
ATC code
V08CA09 — GADOBUTROL
Marketing authorisation
31449
MA holder
BAYER AB
MA country
Denmark
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Aarhus University

Sponsor organisation
Aarhus University
Address
Palle Juul-Jensens Boulevard 82
City
Aarhus N
Postcode
8200
Country
Denmark

Scientific contact point

Organisation
Aarhus University
Contact name
Mattias Kristensen

Public contact point

Organisation
Aarhus University
Contact name
Mattias Kristensen

Third parties 1

OrganisationCity, countryDuties
Aarhus University
ORG-100028380
Aarhus N, Denmark On site monitoring, Code 8

Locations

1 EU/EEA country · 2 investigational sites

By country

CountryMS statusPlanned subjectsSites
Denmark Ongoing, recruitment ended 39 2
Rest of world 0

Investigational sites

Denmark

2 sites · Ongoing, recruitment ended
Aarhus University Hospital
Respiratory Diseases and Allergy, Palle Juul-Jensens Boulevard 99, 8200, Aarhus N
Aarhus University
The MR Research Centre, Palle Juul-Jensens Boulevard 82, 8200, Aarhus N

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Denmark 2023-10-02 2023-10-05 2025-11-19

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 12 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) Protocol 129Xe MR IPF 7.0
Recruitment arrangements (for publication) Recruitment arrangements 2
Subject information and informed consent form (for publication) Dine rettigheder som forsgsperson i forsg med medicin 2
Subject information and informed consent form (for publication) Fr du beslutter dig 1
Subject information and informed consent form (for publication) Interview Guide 2022-502512-36-00 1
Subject information and informed consent form (for publication) K-BILD 1
Subject information and informed consent form (for publication) L-PF Impacts 1
Subject information and informed consent form (for publication) L-PF Symptoms 1
Subject information and informed consent form (for publication) Patientinformation 4.1
Subject information and informed consent form (for publication) Patientsamtykke 3
Subject information and informed consent form (for publication) SOBQ 1
Synopsis of the protocol (for publication) Protocol synopsis 4

Application history

3 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2022-11-11 Denmark Acceptable
2023-03-06
2023-03-06
2 SUBSTANTIAL MODIFICATION SM-3 2023-11-10 Denmark Acceptable
2024-01-12
2024-01-16
3 SUBSTANTIAL MODIFICATION SM-4 2024-12-09 Denmark Acceptable
2025-01-31
2025-01-31