CAR123 T cell treatment of relapsed/refractory hematologic malignancies.

2022-503165-30-00 Protocol UHKT-CAR123-01 Human pharmacology (Phase I) - First administration to humans Ongoing, recruiting

Start 23 Oct 2024 · Status Ongoing, recruiting · 1 EU/EEA countries · 1 sites · Protocol UHKT-CAR123-01

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - First administration to humans
Status Ongoing, recruiting
Participants planned 18
Countries 1
Sites 1

Relapsed/refractory CD123+ hematological malignancies: Acute Myeloid Leukemia, Myelodysplastic Syndrome, Blastic Plasmacytoid Dendritic Cell Neoplasm, Acute Lymphoblastic Leukemia.

Key facts

Sponsor
Institute Of Hematology And Blood Transfusion
Participant type
Patients
Age range
65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Neoplasms [C04], Diseases [C] - Hemic and Lymphatic Diseases [C15]
Trial duration
23 Oct 2024 → ongoing
Decision date (initial)
2024-09-05
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
Yes

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Relapsed/refractory CD123+ hematological malignancies: Acute Myeloid Leukemia, Myelodysplastic Syndrome, Blastic Plasmacytoid Dendritic Cell Neoplasm, Acute Lymphoblastic Leukemia.

VersionLevelCodeTermSystem organ class
20.0 HLGT 10024324 Leukaemias 10029104

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Institute Of Hematology And Blood Transfusion

2 Total trials 2 Recruiting
Academic / Non-commercial
Sponsor organisation
Institute Of Hematology And Blood Transfusion
Address
U Nemocnice 2094/1, Nove Mesto Nove Mesto
City
Prague
Postcode
128 00
Country
Czechia

Scientific contact point

Organisation
Institute Of Hematology And Blood Transfusion
Contact name
Dr. Petr Lesný, Imunoterapie ÚHKT

Public contact point

Organisation
Institute Of Hematology And Blood Transfusion
Contact name
Information site

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Czechia Ongoing, recruiting 18 1
Rest of world 0

Investigational sites

Czechia

1 site · Ongoing, recruiting
Institute Of Hematology And Blood Transfusion
JIHeP, U Nemocnice 2094/1, Nove Mesto, Prague

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Czechia 2024-10-23 2024-10-23

Application history

2 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-05-30 Czechia Acceptable
2024-09-02
2024-09-05
2 NON SUBSTANTIAL MODIFICATION NSM-1 2026-05-21 Czechia Acceptable
2024-09-02
2026-05-21