A Phase 1/2 Open-Label, Multicenter Study of INCB000928 Administered as a Monotherapy or in Combination With Ruxolitinib in Participants With Anemia Due to Myeloproliferative Disorders

2023-503624-83-00 Protocol INCB 00928-104 Phase I and Phase II (Integrated) - Other Ongoing, recruitment ended

Start 16 Aug 2021 · Status Ongoing, recruitment ended · 2 EU/EEA countries · 8 sites · Protocol INCB 00928-104

Overview

Sponsor-declared trial summary

Phase Phase I and Phase II (Integrated) - Other
Status Ongoing, recruitment ended
Participants planned 130
Countries 2
Sites 8

Anaemia associated with myelofibrosis

Key facts

Sponsor
Incyte Corp.
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Neoplasms [C04]
Trial duration
16 Aug 2021 → ongoing
Decision date (initial)
2024-09-05
Transition trial
Yes
Low-intervention
No
Rare-disease indication
No
Vulnerable population
No

External identifiers

EU CT number
2023-503624-83-00
EudraCT number
2020-004029-21

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Anaemia associated with myelofibrosis

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Incyte Corp.

Sponsor organisation
Incyte Corp.
Address
1801 Augustine Cut Off
City
Wilmington
Postcode
19803-4404
Country
United States

Scientific contact point

Organisation
Incyte Corp.
Contact name
Clinical Trial Information

Public contact point

Organisation
Incyte Corp.
Contact name
Clinical Trial Information

Locations

2 EU/EEA countries · 8 investigational sites

By country

CountryMS statusPlanned subjectsSites
France Ended 40 3
Italy Ongoing, recruitment ended 50 5
Rest of world
United States
40

Investigational sites

France

3 sites · Ended
Hopital Saint Louis
Centre d'Investigations Cliniques, 1 Avenue Claude Vellefaux, 75010, Paris
Institut Paoli Calmettes
Hematology, 232 Boulevard De Sainte Marguerite, Bp 156, Marseille
Centre Hospitalier Universitaire D'Angers
Blood diseases, 4 Rue Larrey, 49100, Angers

Italy

5 sites · Ongoing, recruitment ended
Azienda Ospedaliero-Universitaria Di Bologna IRCCS Istituto Di Ricerca E Di Cura A Carattere Scientifico
Complex Operational Unit (UOC) Hematology - Via G. Massarenti 9 40138 Bologna Italy, Via Pietro Albertoni 15, 40138, Bologna
Azienda Socio Sanitaria Territoriale Papa Giovanni Xxiii
Departmental of Oncology and Hematology, Piazza Oms 1, 24127, Bergamo
Careggi University Hospital
Departmental Hospital Section (SOD) of Hematology, Largo Giovanni Alessandro Brambilla 3, 50134, Florence
Hospital Santa Maria Della Misericordia
Departmental of Hematology, Piazzale Giorgio Menghini 1, 06129, Perugia
Azienda Ospedaliero-Universitaria San Luigi Gonzaga
Dpt of Clinical and Biological Sciences, Regione Gonzole 10, 10043, Orbassano

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
France 2021-08-16 2025-06-16 2021-08-16 2024-11-12
Italy 2021-12-20 2021-12-20 2024-11-12

Application history

8 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-06-28 France Acceptable
2024-09-05
2024-09-05
2 NON SUBSTANTIAL MODIFICATION NSM-1 2025-03-11 Acceptable
2024-09-05
2025-03-11
3 NON SUBSTANTIAL MODIFICATION NSM-2 2025-07-07 Acceptable
2024-09-05
2025-07-07
4 NON SUBSTANTIAL MODIFICATION NSM-3 2025-07-15 Acceptable
2024-09-05
2025-07-15
5 NON SUBSTANTIAL MODIFICATION NSM-4 2025-07-21 Acceptable
2024-09-05
2025-07-21
6 NON SUBSTANTIAL MODIFICATION NSM-5 2025-07-31 Acceptable
2024-09-05
2025-07-31
7 NON SUBSTANTIAL MODIFICATION NSM-6 2025-12-03 Acceptable
2024-09-05
2025-12-03
8 NON SUBSTANTIAL MODIFICATION NSM-7 2026-03-19 Acceptable
2024-09-05
2026-03-19