Plethysmography with acetylcholin and carbacholin – A clinical method study

2023-503908-87-00 Therapeutic exploratory (Phase II) Ended

Start 2 Jun 2023 · End 17 Aug 2023 · Status Ended · 1 EU/EEA countries · 1 sites

Overview

Sponsor-declared trial summary

Phase Therapeutic exploratory (Phase II)
Status Ended
Participants planned 1
Countries 1
Sites 1

Vascular dysfunction

To assess whether carbachol is comparable to acetylcholine for evaluating realtive and absolute forearm blood flow (FBF). FBF is evaluated by classic venous occlusion-plethysmography.

Key facts

Sponsor
Regionshospitalet Godstrup
Participant type
Healthy volunteers
Age range
18-64 years
Gender
Male and Female
Therapeutic area
Phenomena and Processes [G] - Circulatory and Respiratory Physiological Phenomena [G09], Diseases [C] - Cardiovascular Diseases [C14]
Trial duration
2 Jun 2023 → 17 Aug 2023
Decision date (initial)
2023-05-25
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
No

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Dose response, Pharmacodynamic, Pharmacokinetic

To assess whether carbachol is comparable to acetylcholine for evaluating realtive and absolute forearm blood flow (FBF). FBF is evaluated by classic venous occlusion-plethysmography.

Conditions and MedDRA coding

Vascular dysfunction

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 4

  1. Healthy men or women
  2. Age between 18-40 years
  3. Fertile women has to receive contraceptive treatment
  4. Body mass index (BMI) between 18.5-30 kg/m2

Exclusion criteria 9

  1. Arterial hypertension defined as office blood pressure above 140 mmHg systolic and/or 90 mmHg diastolic
  2. Significant clinical signs of disease in heart, lungs, liver, kidney, endocrine organs or brain or neoplastic disease
  3. Clinical significant abnormalities in blood- or urine samples collected at the screening examination
  4. Clinical significant abnormalities in electrocardiogram (ECG) made at the screening examination
  5. Abuse of alcohol, defined as more than 14 units per week
  6. Abuse of drugs
  7. Pharmacological treatment, contraveptive medicine exepted
  8. Smoking
  9. Pregnancy or breast feeding

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Relative and absolute forearm blood flow (FBF)

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 2

Miochol®-E, 20mg, Powder and Solvent for instillation solution for intraocular use

PRD295720 · Product

Active substance
Acetylcholine Chloride
Pharmaceutical form
INTRAOCULAR INSTILLATION SOLUTION
Route of administration
INTRAARTERIAL USE
Max daily dose
3.1 mg milligram(s)
Max total dose
3.1 mg milligram(s)
Max treatment duration
1 Day(s)
Authorisation status
Authorised
ATC code
S01EB09 — ACETYLCHOLINE
Marketing authorisation
PL13757/0017
MA holder
DR. GERHARD MANN CHEM.-PHARM. FABRIK GMBH
MA country
XI
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

MIOSTAT 0,01 % intraokulare Injektionslösung

PRD7430464 · Product

Active substance
Carbachol
Pharmaceutical form
INTRAOCULAR INSTILLATION SOLUTION
Route of administration
INTRAARTERIAL USE
Max daily dose
67 µg microgram(s)
Max total dose
67 µg microgram(s)
Max treatment duration
1 Day(s)
Authorisation status
Authorised
ATC code
S01EB02 — CARBACHOL
Marketing authorisation
BE138537
MA holder
ALCON NV
MA country
Belgium
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Regionshospitalet Godstrup

Sponsor organisation
Regionshospitalet Godstrup
Address
Hospitalsparken 15
City
Herning
Postcode
7400
Country
Denmark

Scientific contact point

Organisation
Regionshospitalet Godstrup
Contact name
Didde Kidmose Kristensen, Universitetsklinik i Nyresygdomme og Blodtryksforhøjelse

Public contact point

Organisation
Regionshospitalet Godstrup
Contact name
Didde Kidmose Kristensen, Universitetsklinik i Nyresygdomme og Blodtryksforhøjelse

Third parties 1

OrganisationCity, countryDuties
Aarhus University
ORG-100028380
Aarhus N, Denmark On site monitoring

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Denmark Ended 1 1
Rest of world 0

Investigational sites

Denmark

1 site · Ended
Aarhus University Hospital
Renal Medicine, Palle Juul-Jensens Boulevard 99, 8200, Aarhus N

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Denmark 2023-06-02 2023-08-17 2023-06-02 2023-08-10

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Summary of results Art. 37(4) CTR

TitleSubmission dateStatusType
Resumé af resultater 2023-503908-87-00
SUM-41349
2024-08-16T18:42:45 Submitted Summary of Results

Layperson summary Annex V

TitleSubmission dateStatusType
Resumé for lægmænd 2023-503908-87-00 2024-08-16T18:43:36 Submitted Laypersons Summary of Results

Documents 2 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Laypersons summary of results (for publication) Resume for lgmnd af resultaterne af det kliniske forsg 2023-503908-87-00 1
Summary of results (for publication) Resume af resultater PACCA 2023-503908-87-00 1

Application history

2 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-02-23 Denmark Acceptable
2023-05-25
2023-05-25
2 NON SUBSTANTIAL MODIFICATION NSM-1 2023-05-26 Denmark Acceptable
2023-05-25
2023-05-26