Adjuvant instillations in intermediate risk NMIBC: A Study comparIng Gemcitabine and MitomYciN (SIGYN-trial)

2023-504945-30-00 Therapeutic confirmatory (Phase III) Ongoing, recruitment ended

Start 16 Mar 2021 · Status Ongoing, recruitment ended · 1 EU/EEA countries · 10 sites

Overview

Sponsor-declared trial summary

Phase Therapeutic confirmatory (Phase III)
Status Ongoing, recruitment ended
Participants planned 340
Countries 1
Sites 10

Primary or recurrent non-muscle invasive bladder cancer with intermediate risk of recurrence after transurethral tumour resection

Investigate if adjuvant gemcitabine improves recurrence free survival compared to adjuvant mitomycin

Key facts

Sponsor
Region Skane, Region Skane
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Neoplasms [C04]
Trial duration
16 Mar 2021 → ongoing
Decision date (initial)
2024-08-30
Transition trial
Yes
Low-intervention
No
Rare-disease indication
No
Vulnerable population
Yes
Funding sources
Cancerfonden

External identifiers

EU CT number
2023-504945-30-00
EudraCT number
2020-001728-33

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Efficacy

Investigate if adjuvant gemcitabine improves recurrence free survival
compared to adjuvant mitomycin

Secondary objectives 1

  1. Secondary objectives are local side effects and HRQoL two weeks after the last instillation, progression-free survival, health economy and adverse events

Conditions and MedDRA coding

Primary or recurrent non-muscle invasive bladder cancer with intermediate risk of recurrence after transurethral tumour resection

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 1

  1. Primary and recurrent non muscle invasive bladder cancer with intermediate risk of recurrence

Exclusion criteria 5

  1. Age below 18 years of age
  2. lack of informed consent
  3. Known allergy to either mitomycin or gemcitabine
  4. Severe incontinence
  5. Cronic urethral catheter

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Recurrence-free survival

Secondary endpoints 1

  1. Local toxicity and HRQol two weeks after last installation, Progression-free survival, Health economy, Adverse events

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 1

Gemcitabine Accord 100 mg/ml Koncentrat till infusionsvätska, lösning

PRD1980140 · Product

Active substance
Gemcitabine
Pharmaceutical form
SOLUTION FOR INFUSION
Route of administration
INTRAVESICAL USE
Max daily dose
1000 mg milligram(s)
Max total dose
6000 mg milligram(s)
Max treatment duration
6 Week(s)
Authorisation status
Authorised
ATC code
L01BC05 — GEMCITABINE
Marketing authorisation
45507
MA holder
ACCORD HEALTHCARE B.V.
MA country
Sweden
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Comparator 1

Mitomycin medac, 40 mg, pulver och vätska till intravesikal lösning

PRD3677051 · Product

Active substance
Mitomycin
Substance synonyms
MITOMYCIN C
Pharmaceutical form
INTRAVESICAL SOLUTION
Route of administration
INTRAVESICAL USE
Max daily dose
40 mg milligram(s)
Max total dose
240 mg milligram(s)
Max treatment duration
6 Week(s)
Authorisation status
Authorised
ATC code
L01DC03 — MITOMYCIN
Marketing authorisation
50421
MA holder
MEDAC GESELLSCHAFT FÜR KLINISCHE SPEZIALPRÄPARATE MBH (WEDEL)
MA country
Sweden
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Region Skane

Sponsor organisation
Region Skane
Address
Dockplatsen 26, Malmo S:t Petri Malmo S:t Petri
City
Malmo
Postcode
211 74
Country
Sweden

Scientific contact point

Organisation
Region Skane
Contact name
Fredrik Liedberg

Public contact point

Organisation
Region Skane
Contact name
Fredrik Liedberg

Third parties 1

OrganisationCity, countryDuties
Region Skane Skanes Universitetssjukhus
ORG-100011290
Lund, Sweden On site monitoring, Data management

Region Skane

Sponsor organisation
Region Skane
Address
Dockplatsen 26, Malmo S:t Petri Malmo S:t Petri
City
Malmo
Postcode
211 74
Country
Sweden

Locations

1 EU/EEA country · 10 investigational sites

By country

CountryMS statusPlanned subjectsSites
Sweden Ongoing, recruitment ended 340 10
Rest of world 0

Investigational sites

Sweden

10 sites · Ongoing, recruitment ended
Region Skane - Skanes Universitetssjukhus
Urologkliniken Jan Waldenströms gata 5, St. Johns, Fritz Bauers Gata 5, Malmo
Region Skane Helsingborg Hospital
Urologikliniken, Charlotte Yhlens Gata 10, Helsingborgs Maria, Helsingborg
Region Skane Angelholms Sjukhus
Urologmottagningen, Landshovdingevagen 7e, 262 52, Angelholm
Region Kronoberg
Urologmottagningen Ljungby lasarett, Kyrkogatan 2, Ljungby, Nygatan 20, Vaxjo Stads- Och Domkyrkofors., Vaxjo
Region Oerebro Laen
Urologkliniken, Universitetssjukhuset Örebro, Södra Grev Rosengatan, Sodra Grev Rosengatan, 701 85, Orebro
Region Kronoberg
Kirurgmottagningen, Centrallasarettet Växjö, Strandvägen 8, Växjö, Nygatan 20, Vaxjo Stads- Och Domkyrkofors., Vaxjo
Region Joenkoepings Laen
Urologmottagningen, Värnamo sjukhus, Doktorsgatan 5, 331 56, Varnamo
Region Joenkoepings Laen
Urologmottagningen, Länssjukhuset Ryhov, Lanssjukhuset Ryhov, Sjukhusgatan, Jonkoping
Region Joenkoepings Laen
Urologmottagningen, Höglandssjukhuset, Vastanagatan 9, 575 33, Eksjo
Region Skane Lasarettet I Landskrona
Urologimottagningen, Vattenverksallen 15, 261 36, Landskrona

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Sweden 2021-03-16 2021-04-16 2025-08-19

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 8 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) D1_Protocol 2023-504945-30-00 1
Protocol (for publication) D4_EQ-5D-5L_SE 1
Protocol (for publication) D4_NMIBC24_SE 1
Protocol (for publication) D4_qlq_c30_SE 1
Recruitment arrangements (for publication) K1_Recruitment arrangements_SE_2023-504945-30-00 1
Subject information and informed consent form (for publication) L1_SIS and ICF 1
Summary of Product Characteristics (SmPC) (for publication) E2_SmPC Mitomycin 1
Synopsis of the protocol (for publication) D1_Protocol synopsis SE 2023-504945-30-00 1

Application history

1 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-08-20 Sweden Acceptable with conditions
2024-08-30
2024-08-30