A Phase 1/2a Study Evaluating the Effects of ARO-MMP7 Inhalation Solution in Healthy Subjects and Patients with Idiopathic Pulmonary Fibrosis

2023-504964-41-00 Protocol AROMMP7-1001 Phase I and Phase II (Integrated) - First administration to humans Ended

Start 6 Nov 2024 · End 6 Oct 2025 · Status Ended · 3 EU/EEA countries · 11 sites · Protocol AROMMP7-1001

Overview

Sponsor-declared trial summary

Phase Phase I and Phase II (Integrated) - First administration to humans
Status Ended
Participants planned 97
Countries 3
Sites 11

Idiopathic pulmonary fibrosis

Key facts

Sponsor
Arrowhead Pharmaceuticals Inc.
Participant type
Healthy volunteers, Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Respiratory Tract Diseases [C08]
Trial duration
6 Nov 2024 → 6 Oct 2025
Decision date (initial)
2023-10-09
Transition trial
No
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
Yes

External identifiers

EU CT number
2023-504964-41-00
WHO UTN
U1111-1281-3043
ClinicalTrials.gov
NCT05537025

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Idiopathic pulmonary fibrosis

VersionLevelCodeTermSystem organ class
21.1 PT 10021240 Idiopathic pulmonary fibrosis 100000004855

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Arrowhead Pharmaceuticals Inc.

Sponsor organisation
Arrowhead Pharmaceuticals Inc.
Address
177 East Colorado Boulevard Suite 700
City
Pasadena
Postcode
91105-1976
Country
United States

Scientific contact point

Organisation
Arrowhead Pharmaceuticals Inc.
Contact name
Medical Department

Public contact point

Organisation
Arrowhead Pharmaceuticals Inc.
Contact name
Regulatory Unit

Locations

3 EU/EEA countries · 11 investigational sites

By country

CountryMS statusPlanned subjectsSites
Denmark Ended 2 2
Italy Ended 6 6
Spain Ended 7 3
Rest of world
New Zealand, United Kingdom
82

Investigational sites

Denmark

2 sites · Ended
Odense University Hospital
Respiratory Medicine, Indgang 87-88, Kloevervaenget 2, Odense C
Rigshospitalet
Pneumology Service - Lung transplantation section, Blegdamsvej 9, 2100, Copenhagen Oe

Italy

6 sites · Ended
Azienda Ospedaliera Dei Colli
Clinical Medecine and Surgery, Via Leonardo Bianchi, 80131, Naples
Careggi University Hospital
Interventional Pulmonology Unit, Largo Giovanni Alessandro Brambilla 3, 50134, Florence
Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico
UOC of Bronchopneumology, Via Francesco Sforza 28, 20122, Milan
Ospedale Giovan Battista Morgagni-Luigi Pierantoni Di Forlì
Pneumology Unit, Via Carlo Forlanini 34, 47121, Forli'
Multimedica S.p.A.
Division of Internal Medicine and the Division of Pulmonary Disease Intensive Respiratory Care Unit, Via San Vittore 12, 20123, Milan
Azienda Ospedaliero Universitaria Delle Marche
Respiratory Medicine Unit, Via Conca 71, 60126, Ancona

Spain

3 sites · Ended
Hospital Universitario Marques De Valdecilla
Pneumology Service, Avenida Valdecilla Sn, 39008, Santander
Pectus Respiratory Health S.L.
Pneumology Service, Calle Del Doctor Roux 78, 08017, Barcelona
Hospital Universitario Central De Asturias
Pneumology Service, Avenida De Roma S/n, 33011, Oviedo

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Denmark 2024-04-18 2025-07-30 2024-06-03 2025-07-30
Italy 2024-11-28 2025-07-30
Spain 2023-12-11 2025-07-30 2024-03-25 2025-07-30

Oversight and notifications

Regulatory notifications under CTR Articles 38, 52, 53, 54 and 77

Temporary halts 2 · Art. 38 CTR

Temporary halt TH-55769

Halt date
2024-11-01
Member states concerned
Spain
Publication date
2024-11-05
Reason
Sponsor decision
Explanation
Temporarily pausing enrollment in limited countries until the investigational medicinal product dossier (IMPD), which is currently being evaluated by regulators, is approved.
Benefit-risk balance changed
No
Treatment stopped
No

Temporary halt TH-55767

Halt date
2024-11-01
Member states concerned
Denmark
Publication date
2024-11-05
Reason
Sponsor decision
Explanation
Temporarily pausing enrollment in limited countries until the investigational medicinal product dossier (IMPD), which is currently being evaluated by regulators, is approved.
Benefit-risk balance changed
No
Treatment stopped
No

Application history

8 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-06-19 Spain Acceptable with conditions
2023-10-06
2023-10-06
2 SUBSTANTIAL MODIFICATION SM-1 2023-12-22 Spain Acceptable
2024-04-01
2024-04-01
3 SUBSTANTIAL MODIFICATION SM-2 2024-05-06 Spain Acceptable
2024-07-03
2024-07-03
4 NON SUBSTANTIAL MODIFICATION NSM-2 2024-09-04 Acceptable
2024-07-03
2024-09-04
5 SUBSTANTIAL MODIFICATION SM-4 2024-09-06 Spain Acceptable
2024-11-06
2024-11-06
6 SUBSTANTIAL MODIFICATION SM-5 2024-11-19 Acceptable 2024-12-20
7 NON SUBSTANTIAL MODIFICATION NSM-3 2025-01-16 Spain 2025-01-16
8 SUBSTANTIAL MODIFICATION SM-6 2025-01-31 Spain Acceptable
2025-04-12
2025-04-12