A Phase 1 Study of JNJ-88549968, a T-cell Redirecting Antibody, for CALR-mutated Myeloproliferative Neoplasms

2023-505584-36-00 Protocol 88549968MPN1001 Human pharmacology (Phase I) - First administration to humans Ongoing, recruiting

Start 30 Jul 2024 · Status Ongoing, recruiting · 4 EU/EEA countries · 12 sites · Protocol 88549968MPN1001

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - First administration to humans
Status Ongoing, recruiting
Participants planned 220
Countries 4
Sites 12

CALR-mutated Myeloproliferative Neoplasms

Key facts

Sponsor
Janssen - Cilag International
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Neoplasms [C04]
Trial duration
30 Jul 2024 → ongoing
Decision date (initial)
2024-02-26
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
No

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

CALR-mutated Myeloproliferative Neoplasms

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Janssen - Cilag International

Sponsor organisation
Janssen - Cilag International
Address
Turnhoutseweg 30
City
Beerse
Postcode
2340
Country
Belgium

Scientific contact point

Organisation
Janssen - Cilag International
Contact name
CTIS Point of Contact

Public contact point

Organisation
Janssen - Cilag International
Contact name
CTIS Point of Contact

Locations

4 EU/EEA countries · 12 investigational sites

By country

CountryMS statusPlanned subjectsSites
France Ongoing, recruiting 9 2
Germany Ongoing, recruiting 27 6
Italy Ongoing, recruiting 7 2
Spain Ongoing, recruiting 7 2
Rest of world
Canada, United Kingdom, Israel, Japan, United States
170

Investigational sites

France

2 sites · Ongoing, recruiting
Assistance Publique Hopitaux De Paris
Centre d'investigation Clinique, 1 Avenue Claude Vellefaux, 75010, Paris
Hospices Civils De Lyon
Service Hématologie, 165 Chemin Du Grand Revoyet, 69310, Pierre-Benite

Germany

6 sites · Ongoing, recruiting
Universitaetsklinikum Aachen AöR
Klinik für Hämatologie, Onkologie, Hämostaseologie und Stammzelltransplantation (Med. Klinik IV), Pauwelsstrasse 30, 52074, Aachen
Universitaetsklinikum Regensburg AöR
Klinik und Poliklinik für Innere Medizin III, Hämatologie und Internistische Onkologie, Franz-Josef-Strauss-Allee 11, Grass-Oberisling, Regensburg
Medizinische Hochschule Hannover
Hämatologie, Hämostaseologie, Onkologie und Stammzelltransplantation, Carl-Neuberg-Strasse 1, Gross Buchholz, Hanover
Universitaetsklinikum Essen AöR
Klinik für Hämatologie und Stammzelltransplantation, Hufelandstrasse 55, Holsterhausen, Essen
Universitaetsklinikum Heidelberg AöR
Zentrum für Innere Medizin, Klinik für Hämatologie, Onkologie und Rheumatologie, Innere Medizin V, Im Neuenheimer Feld 410, Neuenheim, Heidelberg
Charite Universitaetsmedizin Berlin KöR
Am Campus Benjamin Franklin, Medizinische Klinik mit Schwerpunkt Hämatologie und Onkologie, Hindenburgdamm 30, Lichterfelde, Berlin

Italy

2 sites · Ongoing, recruiting
Azienda Ospedaliero-Universitaria Di Bologna IRCCS Istituto Di Ricerca E Di Cura A Carattere Scientifico
UO Ematologia, Via Pietro Albertoni 15, 40138, Bologna
Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico
SC Ematologia, Via Francesco Sforza 28, 20122, Milan

Spain

2 sites · Ongoing, recruiting
Hospital Clinico Universitario De Valencia
Hematology, Avenida Blasco Ibanez 17, 46010, Valencia
Institut Catala D'oncologia
Hematology, Carretera Canyet S/n, 08916, Badalona

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
France 2024-07-30 2024-07-30
Germany 2024-09-04 2024-09-04
Italy 2026-02-19 2026-02-19
Spain 2024-10-21 2024-10-21

Application history

10 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-10-17 Spain Acceptable
2024-02-16
2024-02-16
2 NON SUBSTANTIAL MODIFICATION NSM-1 2024-03-01 Spain Acceptable
2024-02-16
2024-03-01
3 NON SUBSTANTIAL MODIFICATION NSM-2 2024-03-11 Acceptable
2024-02-16
2024-03-11
4 SUBSEQUENT ADDITION OF MSC APP-4 2024-03-25 Acceptable
2024-02-16
2024-06-13
5 SUBSTANTIAL MODIFICATION SM-2 2024-07-02 Spain Acceptable
2024-08-26
2024-08-26
6 NON SUBSTANTIAL MODIFICATION NSM-3 2024-11-08 Spain Acceptable
2024-08-26
2024-11-08
7 SUBSTANTIAL MODIFICATION SM-4 2024-12-17 Spain Acceptable
2025-04-11
2025-04-11
8 SUBSTANTIAL MODIFICATION SM-5 2025-04-15 Acceptable 2025-06-13
9 SUBSEQUENT ADDITION OF MSC APP-9 2025-04-17 Acceptable
2025-04-11
2025-07-07
10 SUBSTANTIAL MODIFICATION SM-6 2026-02-03 Spain Acceptable
2026-04-20
2026-04-22