Pharmacokinetic comparison of efanesoctocog alfa vs other EHL-rFVIII products in participants with severe haemophilia A

2023-505801-17-00 Protocol Sobi.BIVV001-003 Human pharmacology (Phase I) - Bioequivalence study Ended

Start 15 Jan 2025 · End 21 May 2026 · Status Ended · 4 EU/EEA countries · 9 sites · Protocol Sobi.BIVV001-003

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - Bioequivalence study
Status Ended
Participants planned 36
Countries 4
Sites 9

Haemophilia A

Key facts

Sponsor
Swedish Orphan Biovitrum AB (publ)
Participant type
Patients
Age range
18-64 years
Gender
Male
Therapeutic area
Diseases [C] - Congenital, Hereditary, and Neonatal Diseases and Abnormalities [C16]
Trial duration
15 Jan 2025 → 21 May 2026
Decision date (initial)
2025-12-18
Transition trial
No
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
No

External identifiers

EU CT number
2023-505801-17-00
WHO UTN
U1111-1292-6071

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Haemophilia A

VersionLevelCodeTermSystem organ class
20.0 LLT 10018937 Haemophilia A 10010331

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Swedish Orphan Biovitrum AB (publ)

Sponsor organisation
Swedish Orphan Biovitrum AB (publ)
Address
-
City
Stockholm
Postcode
112 76
Country
Sweden

Scientific contact point

Organisation
Swedish Orphan Biovitrum AB (publ)
Contact name
Contact point

Public contact point

Organisation
Swedish Orphan Biovitrum AB (publ)
Contact name
Contact point

Locations

4 EU/EEA countries · 9 investigational sites

By country

CountryMS statusPlanned subjectsSites
Bulgaria Ended 12 1
Germany Ended 7 2
Italy Ended 7 3
Spain Ended 10 3
Rest of world 0

Investigational sites

Bulgaria

1 site · Ended
Specialized Hospital For Active Treatment Of Hematological Diseases EAD
Third Department of Clinical Hematology at Clinical Hematology Clinic, Bulevard Kliment Ohridski 1a, 1797, Sofiya

Germany

2 sites · Ended
Universitaetsklinikum Frankfurt AöR
Hematology, Theodor-Stern-Kai 7, 60590, Frankfurt Am Main
Universitaetsklinikum Bonn AöR
Experimental Haematology and Transfusion Medicine, Venusberg-Campus 1, Venusberg, Bonn

Italy

3 sites · Ended
Azienda Ospedaliera Universitaria Federico II Di Napoli
Unit of Innovative Therapies for Genetic and Metabolic Diseases, Via Sergio Pansini 5, 80131, Naples
Humanitas Research Hospital
Phase I Unit, Via Alessandro Manzoni 56, 20089, Rozzano
Azienda Ospedaliero Universitaria Careggi
Center for Bleeding Clinical Trial Unit-1 (CTU-1), Largo Giovanni Alessandro Brambilla 3, 50134, Florence

Spain

3 sites · Ended
Complejo Hospitalario Universitario Juan Canalejo
Hematology, Barrio As Xubias 84, 15006, A Coruna
Hospital Unviersitario Miguel Servet
Hematology and Hemotherapy Department, Paseo De Isabel La Catolica 1-3, 50009, Zaragoza
Hospital Universitario Y Politecnico La Fe
Hemostasis and Thrombosis Unit, Avenida De Fernando Abril Martorell 106, 46026, Valencia

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Bulgaria 2026-02-04 2026-05-21 2026-02-19 2026-04-30
Germany 2025-01-15 2026-05-21 2025-01-20 2026-04-30
Italy 2025-01-15 2026-05-21 2025-02-19 2026-04-30
Spain 2025-01-15 2026-05-21 2025-02-04 2026-04-30

Application history

10 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-11-23 Germany Acceptable
2024-04-02
2024-04-03
2 SUBSTANTIAL MODIFICATION SM-1 2024-07-08 Germany Acceptable
2024-09-02
2024-09-03
3 NON SUBSTANTIAL MODIFICATION NSM-1 2024-10-03 Germany Acceptable
2024-09-02
2024-10-03
4 NON SUBSTANTIAL MODIFICATION NSM-2 2025-01-21 Germany Acceptable
2024-09-02
2025-01-21
5 NON SUBSTANTIAL MODIFICATION NSM-3 2025-02-25 Germany Acceptable
2024-09-02
2025-02-25
6 SUBSTANTIAL MODIFICATION SM-4 2025-04-30 Acceptable 2025-05-19
7 SUBSTANTIAL MODIFICATION SM-5 2025-08-22 Germany Acceptable
2025-10-06
2025-10-08
8 SUBSTANTIAL MODIFICATION SM-6 2025-10-16 Acceptable 2025-11-20
9 SUBSEQUENT ADDITION OF MSC APP-9 2025-10-17 Acceptable
2025-10-06
2025-12-18
10 SUBSTANTIAL MODIFICATION SM-7 2026-03-06 Acceptable 2026-06-01