A randomized controlled trial comparing sequential of two shots of CFA vs CFA + rFSH for Elective Fertility Preservation. The 2-shot protocol.

2023-506162-31-00 Protocol FSD-SEQ-2023-09 Therapeutic confirmatory (Phase III) Ended

Start 12 Dec 2023 · End 9 Sep 2025 · Status Ended · 1 EU/EEA countries · 1 sites · Protocol FSD-SEQ-2023-09

Overview

Sponsor-declared trial summary

Phase Therapeutic confirmatory (Phase III)
Status Ended
Participants planned 194
Countries 1
Sites 1

Infertility

To compare the number of mature oocytes (MII) retrieved after 2-shot sequential administration of Corifollitropin alpha (CFA) and a unique administration of CFA followed by the administration of rFSH daily for ovarian stimulation (OS) in patients undergoing elective fertility preservation in a progestin-primed ovarian …

Key facts

Sponsor
Santiago Dexeus Font Fundacio Privada
Participant type
Patients
Age range
18-64 years
Gender
Female
Therapeutic area
Diseases [C] - Female Urogenital Diseases and Pregnancy Complications [C13]
Trial duration
12 Dec 2023 → 9 Sep 2025
Decision date (initial)
2023-10-26
Transition trial
No
Low-intervention
Yes
Rare-disease indication
No
Vulnerable population
No
Funding sources
ORGANON SPAIN

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Efficacy

To compare the number of mature oocytes (MII) retrieved after 2-shot sequential administration of Corifollitropin alpha (CFA) and a unique administration of CFA followed by the administration of rFSH daily for ovarian stimulation (OS) in patients undergoing elective fertility preservation in a progestin-primed ovarian stimulation (PPOS) protocol and GnRH-agonist (GnRH-a) triggering.

Secondary objectives 5

  1. Total number of oocytes retrieved
  2. Endocrine profile on the day of trigger (FSH, LH, Estradiol, progesterone)
  3. Incidence of OHSS
  4. Quality of life questionnaire “FertiQoL”
  5. Length of stimulation

Conditions and MedDRA coding

Infertility

VersionLevelCodeTermSystem organ class
20.0 LLT 10021930 Infertility NOS 10038604

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 5

  1. AFC ≤ 20
  2. Anti-Mullerian hormone (AMH) ≤ 3ng/ml (AMH result of up to one year will be valid)
  3. Between 18 and 40 years old
  4. BMI > 18 and < 30 kg/m2
  5. Able to come to the Center to comply with the procedures of the study: blood tests, appointments and drug dispensation

Exclusion criteria 7

  1. Medically indicated fertility preservation
  2. AFC > 20
  3. Polycystic ovarian syndrome (PCOS) according to the Rotterdam criteria
  4. FSH ≥ 20
  5. History of untreated autoimmune, endocrine, or metabolic disorders
  6. Contraindication for hormonal treatment
  7. Recent history of severe disease requiring regular treatment (clinically significant concurrent medical condition that could compromise subject safety or interfered with the trial assessment).

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. To compare the number of MII oocytes retrieved after final oocyte maturation with a 2-shot sequential administration of CFA or a unique administration of CFA followed by daily rFSH for controlled ovarian stimulation in patients undergoing elective fertility preservation.

Secondary endpoints 5

  1. Total number of oocytes retrieved
  2. Endocrine profile on the day of trigger (FSH, LH, estradiol, progesterone)
  3. Incidence of OHSS
  4. Quality of life questionnaire “FertiQoL”
  5. Length of stimulation

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 1

Elonva 100 micrograms solution for injection

PRD9049682 · Product

Active substance
Corifollitropin Alfa
Pharmaceutical form
SOLUTION FOR INJECTION
Route of administration
SUBCUTANEOUS INJECTION
Max daily dose
100 µg microgram(s)
Max total dose
100 µg microgram(s)
Max treatment duration
1 Day(s)
Authorisation status
Authorised
ATC code
G03GA09 — -
Marketing authorisation
EU/1/09/609/001
MA holder
N.V. ORGANON
MA country
Norway
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Comparator 1

Puregon 900 IU/1.08 ml solution for injection

PRD9022797 · Product

Active substance
Follitropin Beta
Pharmaceutical form
SOLUTION FOR INJECTION
Route of administration
SOLUTION FOR INJECTION
Max daily dose
200 IU international unit(s)
Max total dose
2000 IU international unit(s)
Max treatment duration
10 Day(s)
Authorisation status
Authorised
ATC code
G03GA06 — FOLLITROPIN BETA
Marketing authorisation
EU/1/96/008/041
MA holder
N.V. ORGANON
MA country
Norway
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Auxiliary 3

Cerazet 75 microgramos comprimidos recubiertos con película

PRD8838400 · Product

Active substance
Desogestrel
Pharmaceutical form
FILM-COATED TABLET
Route of administration
ORAL
Max daily dose
75 µg microgram(s)
Max total dose
750 µg microgram(s)
Max treatment duration
10 Day(s)
Authorisation status
Authorised
ATC code
G03AC09 — DESOGESTREL
Marketing authorisation
62285
MA holder
ORGANONSALUD, S.L.
MA country
Spain
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Elonva 150 micrograms solution for injection

PRD9049686 · Product

Active substance
Corifollitropin Alfa
Pharmaceutical form
SOLUTION FOR INJECTION
Route of administration
SUBCUTANEOUS INJECTION
Max daily dose
150 µg microgram(s)
Max total dose
150 µg microgram(s)
Max treatment duration
1 Day(s)
Authorisation status
Authorised
ATC code
G03GA09 — -
Marketing authorisation
EU/1/09/609/002
MA holder
N.V. ORGANON
MA country
Norway
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Decapeptyl diario 0,1 mg polvo y disolvente para solución inyectable

PRD390680 · Product

Active substance
Triptorelin
Pharmaceutical form
SOLUTION FOR INJECTION
Route of administration
SUBCUTANEOUS INJECTION
Max daily dose
0.1 mg milligram(s)
Max total dose
0.1 mg milligram(s)
Max treatment duration
1 Day(s)
Authorisation status
Authorised
ATC code
L02AE04 — TRIPTORELIN
Marketing authorisation
62.431
MA holder
IPSEN PHARMA SA
MA country
Spain
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Santiago Dexeus Font Fundacio Privada

Sponsor organisation
Santiago Dexeus Font Fundacio Privada
Address
Gran Via De Carles III 71-75
City
Barcelona
Postcode
08028
Country
Spain

Scientific contact point

Organisation
Santiago Dexeus Font Fundacio Privada
Contact name
Unidad Soporte Investigación

Public contact point

Organisation
Santiago Dexeus Font Fundacio Privada
Contact name
Unidad Soporte Investigación

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Spain Ended 194 1
Rest of world 0

Investigational sites

Spain

1 site · Ended
Hospital Universitari Dexeus Grupo Quironsalud
Department of Reproductive Medicine, Calle De Sabino Arana 5-19, 08028, Barcelona

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Spain 2023-12-12 2025-09-09 2023-12-19 2025-08-28

Application history

2 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-08-30 Spain Acceptable
2023-10-20
2023-10-26
2 SUBSTANTIAL MODIFICATION SM-1 2024-04-04 Spain Acceptable 2024-04-17