A study of continued treatment with regorafenib in participants with solid tumors who have participated in other Bayer studies

2023-507084-19-00 Protocol 22551 Therapeutic exploratory (Phase II) Ongoing, recruitment ended

Start 7 Mar 2024 · Status Ongoing, recruitment ended · 2 EU/EEA countries · 5 sites · Protocol 22551

Overview

Sponsor-declared trial summary

Phase Therapeutic exploratory (Phase II)
Status Ongoing, recruitment ended
Participants planned 11
Countries 2
Sites 5

Solid malignant tumors

The primary purpose of the program is to enable participants, currently receiving regorafenib in a Bayer sponsored clinical trial and assessed by the principal investigator to be benefiting, to continue regorafenib treatment after their respective study has met its primary completion date, or main data analysis, or has…

Key facts

Sponsor
Bayer AG
Participant type
Pediatric, Patients
Age range
0-17 years, 18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Neoplasms [C04]
Trial duration
7 Mar 2024 → ongoing
Decision date (initial)
2024-02-19
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
Yes
Funding sources
Bayer AG

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Therapy, Safety

The primary purpose of the program is to enable participants, currently receiving regorafenib in a Bayer sponsored clinical trial and assessed by the principal investigator to be benefiting, to continue regorafenib treatment after their respective study has met its primary completion date, or main data analysis, or has been stopped prematurely and the documentation of safety

Secondary objectives 1

  1. Documentation of tolerability

Conditions and MedDRA coding

Solid malignant tumors

VersionLevelCodeTermSystem organ class
21.1 LLT 10065147 Malignant solid tumor 10029104

Study design 1 period

#TitleAllocationBlindingRoles blindedArms
1 Overall Study
This is an open-label study that will enable participants currently receiving regorafenib in a Bayer-sponsored clinical trial to continue treatment after their respective study has been completed. A completed study is defined as one that has reached the primary completion endpoint, or main data analysis, or has been stopped prematurely, and the respective data have been cleaned.
Not Applicable None Regorafenib: Adult and pediatric patients from completed Bayer-sponsored regorafenib trials who are benefiting from regorafenib treatment.

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 3

  1. Participant is currently participating in any Bayer-sponsored regorafenib study and is receiving regorafenib as study treatment.
  2. Participant is currently benefiting from treatment with regorafenib monotherapy. All participants must meet criteria to initiate a subsequent cycle of therapy, as determined by the guidelines of the feeder protocol.
  3. Any ongoing adverse events that require temporary treatment interruption must be resolved to baseline grade or assessed as stable and not requiring further treatment interruption by the investigator.

Exclusion criteria 4

  1. Ineligibility, for medical reasons, to start the subsequent cycle in the respective feeder study.
  2. Participants with a beta-human chorionic gonadotropin (hCG) test result consistent with pregnancy.
  3. Participants are using one or more of the prohibited medications listed in the respective feeder study protocol.
  4. Participant has been previously permanently discontinued from regorafenib treatment.

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Number of participants with serious adverse events (SAEs) and protocol-specified AEs and their severity

Secondary endpoints 1

  1. Number of participants with dose modifications

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 2

BAY 734506

PRD10079495 · Product

Active substance
Regorafenib
Pharmaceutical form
FILM-COATED TABLET
Route of administration
ORAL USE
Max daily dose
160 mg milligram(s)
Max total dose
93.24 g gram(s)
Max treatment duration
26 Month(s)
Authorisation status
Not Authorised
MA holder
BAYER AG
Paediatric formulation
No
Orphan designation
No

BAY 73-4506

PRD124397 · Product

Active substance
Regorafenib
Pharmaceutical form
FILM-COATED TABLET
Route of administration
ORAL USE
Max daily dose
120 mg milligram(s)
Max total dose
62.16 g gram(s)
Max treatment duration
26 Month(s)
Authorisation status
Not Authorised
MA holder
BAYER HEALTHCARE AG
Paediatric formulation
No
Orphan designation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Bayer AG

Sponsor organisation
Bayer AG
Address
Kaiser-Wilhelm-Allee 1, Wiesdorf Wiesdorf
City
Leverkusen
Postcode
51373
Country
Germany

Scientific contact point

Organisation
Bayer AG
Contact name
Therapeutic Area Head

Public contact point

Organisation
Bayer AG
Contact name
Therapeutic Area Head

Third parties 1

OrganisationCity, countryDuties
Fisher Clinical Services GmbH
ORG-100012942
Allschwil, Switzerland Code 14

Locations

2 EU/EEA countries · 5 investigational sites

By country

CountryMS statusPlanned subjectsSites
France Ongoing, recruitment ended 4 4
Spain Ended 1 1
Rest of world
Korea, Republic of, Japan, India, Taiwan
6

Investigational sites

France

4 sites · Ongoing, recruitment ended
Assistance Publique Hopitaux De Paris
Hepatology department, 12 Avenue Paul Vaillant Couturier, 94800, Villejuif
Hopital Huriez
Department of Digestive Diseases and Nutrition, 1 Place De Verdun, 59045, Lille Cedex
Institut Bergonie
Department of medical oncology, 229 Cours De L Argonne, 33000, Bordeaux
Hopital Beaujon
Digestive oncology, 100 Boulevard Du General Leclerc, 92110, Clichy

Spain

1 site · Ended
Hospital Infantil Universitario Nino Jesus
Pediatric hematology oncology service, Avenida Menendez Pelayo 65, 28009, Madrid

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
France 2024-03-07 2024-03-12 2024-04-23
Spain 2024-03-08 2024-09-23 2024-03-13 2024-03-13

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 9 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) D1_Protocol_EN_2023-507084-19-00_public 2
Recruitment arrangements (for publication) K1_Recruitment arrangements_FR_Recruitment info ICF Procedure_Public 1
Subject information and informed consent form (for publication) L1_ICF_FR_FR_Consent Form for Expecting Parents Female Study Participant_public 1.1
Subject information and informed consent form (for publication) L1_ICF_FR_FR_Consent Form for Expecting Parents Male Study Participant_public 1.1
Subject information and informed consent form (for publication) L1_ICF_FR_FR_Master PIIC_public 1.1
Subject information and informed consent form (for publication) L1_SIS_and_ICF_Study_Update_Public_FR_FR 1.1
Synopsis of the protocol (for publication) D1_Synopsis of Protocol_EN_2023-507084-19-00_public 1
Synopsis of the protocol (for publication) D1_Synopsis of Protocol_ES_ES_2023-507084-19-00_public 1
Synopsis of the protocol (for publication) D1_Synopsis of Protocol_FR_2023-507084-19-00_public 1

Application history

7 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-10-13 France Acceptable
2024-02-19
2024-02-19
2 SUBSTANTIAL MODIFICATION SM-1 2024-02-21 France Acceptable
2024-03-15
2024-03-15
3 NON SUBSTANTIAL MODIFICATION NSM-1 2024-02-21 Acceptable
2024-02-19
2024-02-21
4 SUBSTANTIAL MODIFICATION SM-2 2024-12-03 France Acceptable
2025-01-17
2025-01-17
5 SUBSTANTIAL MODIFICATION SM-3 2025-09-02 France Acceptable 2025-11-12
6 SUBSTANTIAL MODIFICATION SM-4 2025-11-27 France Acceptable
2025-12-23
2026-01-07
7 NON SUBSTANTIAL MODIFICATION NSM-2 2026-02-25 France Acceptable
2025-12-23
2026-02-25