A Phase 1, Randomized, Double-Blind, Placebo-Controlled, Dose-Escalating Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of Single Ascending and Multiple Ascending Doses of Prosetin in Healthy Volunteers and Participants with Amyotrophic Lateral Sclerosis (ALS) with an Optional Open-Label Extended Treatment Period for ALS Participants who Complete 14 Days of Blinded Treatment

2023-507363-20-00 Protocol PRO-101 Human pharmacology (Phase I) - First administration to humans Ongoing, recruitment ended

Start 12 Jul 2024 · Status Ongoing, recruitment ended · 1 EU/EEA countries · 1 sites · Protocol PRO-101

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - First administration to humans
Status Ongoing, recruitment ended
Participants planned 40
Countries 1
Sites 1

Amyotrophic lateral sclerosis (ALS)

Key facts

Sponsor
Projenx Inc.
Participant type
Healthy volunteers, Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Nervous System Diseases [C10]
Trial duration
12 Jul 2024 → ongoing
Decision date (initial)
2024-02-05
Transition trial
No
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
No

External identifiers

EU CT number
2023-507363-20-00
ClinicalTrials.gov
NCT05279755

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Amyotrophic lateral sclerosis (ALS)

VersionLevelCodeTermSystem organ class
21.1 PT 10002026 Amyotrophic lateral sclerosis 100000004852

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Projenx Inc.

Sponsor organisation
Projenx Inc.
Address
3960 Broadway
City
New York
Postcode
10032-1543
Country
United States

Scientific contact point

Organisation
Projenx Inc.
Contact name
VP Research and Development

Public contact point

Organisation
Projenx Inc.
Contact name
VP Research and Development

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Netherlands Ongoing, recruitment ended 14 1
Rest of world
United States, Canada
26

Investigational sites

Netherlands

1 site · Ongoing, recruitment ended
Universitair Medisch Centrum Utrecht
Neurology & Neurosurgery, Universiteitsweg 99/100, 3584 CG, Utrecht

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Netherlands 2024-07-12 2024-07-16 2026-03-11

Application history

7 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-10-11 Netherlands Acceptable
2024-01-29
2024-02-05
2 SUBSTANTIAL MODIFICATION SM-1 2024-04-03 Netherlands Acceptable
2024-06-21
2024-06-21
3 SUBSTANTIAL MODIFICATION SM-2 2024-08-29 Netherlands Acceptable
2024-10-14
2024-10-21
4 NON SUBSTANTIAL MODIFICATION NSM-1 2025-01-30 Netherlands Acceptable
2024-10-14
2025-01-30
5 SUBSTANTIAL MODIFICATION SM-3 2025-05-28 Netherlands Acceptable
2025-07-07
2025-07-10
6 NON SUBSTANTIAL MODIFICATION NSM-2 2025-10-10 Netherlands Acceptable
2025-07-07
2025-10-10
7 SUBSTANTIAL MODIFICATION SM-4 2026-01-19 Netherlands Acceptable
2026-02-19
2026-02-19