Study of PIT565 in relapsed and/or refractory B-cell malignancies

2023-507430-25-00 Protocol CPIT565A12101 Human pharmacology (Phase I) - First administration to humans Ended

Start 3 Oct 2022 · End 9 Jan 2026 · Status Ended · 4 EU/EEA countries · 7 sites · Protocol CPIT565A12101

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - First administration to humans
Status Ended
Participants planned 78
Countries 4
Sites 7

Relapsed and/or refractory B-cell Non-Hodgkin lymphoma (R/R B-NHL) and relapsed and/or refractory B-cell acute lymphoblastic leukemia (R/R B-ALL)

Key facts

Sponsor
Novartis Pharma AG
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Neoplasms [C04]
Trial duration
3 Oct 2022 → 9 Jan 2026
Decision date (initial)
2024-02-14
Transition trial
Yes
Low-intervention
No
Rare-disease indication
No
Vulnerable population
Yes

External identifiers

EU CT number
2023-507430-25-00
EudraCT number
2022-000367-45

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Relapsed and/or refractory B-cell Non-Hodgkin lymphoma (R/R B-NHL) and relapsed and/or refractory B-cell acute lymphoblastic leukemia (R/R B-ALL)

VersionLevelCodeTermSystem organ class
23.0 LLT 10025311 Lymphoma (non-Hodgkin's) 10029104
21.0 LLT 10000844 Acute lymphoblastic leukaemia 10029104

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Novartis Pharma AG

Sponsor organisation
Novartis Pharma AG
Address
Lichtstrasse 35
City
Basel Town
Postcode
4056
Country
Switzerland

Scientific contact point

Organisation
Novartis Pharma AG
Contact name
Novartis Pharma Arzneimittel GmbH

Public contact point

Organisation
Novartis Pharma AG
Contact name
Novartis Pharma Arzneimittel GmbH

Locations

4 EU/EEA countries · 7 investigational sites

By country

CountryMS statusPlanned subjectsSites
Belgium Ended 6 1
France Ended 8 2
Italy Ended 6 2
Spain Ended 12 2
Rest of world
Singapore, Israel, United States, Japan
46

Investigational sites

Belgium

1 site · Ended
Universitair Ziekenhuis Gent
#1000:Hematology, Corneel Heymanslaan 10, 9000, Gent

France

2 sites · Ended
Assistance Publique Hopitaux De Paris
#2001:Unite Hemopathies Lymphoides, 51 Av Du Mal De Lattre De Tassigny, 94000, Creteil
Institut Paoli-Calmettes
#2000:Hematologie 4, 232 Boulevard De Sainte Marguerite, Bp 156, Marseille

Italy

2 sites · Ended
Azienda USL IRCCS Di Reggio Emilia
6002:S.C. Ematologia, Viale Risorgimento 80, 42123, Reggio Emilia
Humanitas Mirasole S.p.A.
6003:U. O. Oncologia Medica ed Ematologia Humanitas Cancer Center, Via Alessandro Manzoni 56, 20089, Rozzano

Spain

2 sites · Ended
Hospital Clinic De Barcelona
#7001:Hematology, Calle Villarroel 170, 08036, Barcelona
Hospital Universitari Vall D Hebron
#7000:Hematology, Edificio Materno-Infantil, Passeig De La Vall D'hebron 119-129, Barcelona

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Belgium 2024-04-23 2024-04-23 2025-01-15
France 2022-10-03 2022-10-03 2025-09-08
Italy 2025-05-08 2025-05-08 2025-08-19
Spain 2023-05-09 2023-05-09 2025-05-27

Application history

4 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-12-20 Belgium Acceptable
2024-02-12
2024-02-14
2 SUBSTANTIAL MODIFICATION SM-1 2024-04-05 Belgium Acceptable
2024-07-01
2024-07-01
3 SUBSTANTIAL MODIFICATION SM-2 2024-12-19 Belgium Acceptable with conditions
2025-03-07
2025-03-10
4 SUBSTANTIAL MODIFICATION SM-3 2025-10-08 Belgium Acceptable
2025-12-18
2025-12-18