Phase Ib Open Label Basket Trial of RAY121 to Inhibit Classical Complement Pathway in Immunological Diseases (RAINBOW Trial)

2023-507692-21-00 Protocol RAY902CT Human pharmacology (Phase I) - Other Ongoing, recruiting

Start 22 Aug 2024 · Status Ongoing, recruiting · 14 EU/EEA countries · 42 sites · Protocol RAY902CT

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - Other
Status Ongoing, recruiting
Participants planned 144
Countries 14
Sites 42

Bullous pemphigoid

Key facts

Sponsor
Chugai Pharmaceutical Co. Ltd.
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Immune System Diseases [C20]
Trial duration
22 Aug 2024 → ongoing
Decision date (initial)
2024-07-15
Transition trial
No
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
No

External identifiers

EU CT number
2023-507692-21-00
ClinicalTrials.gov
NCT06371417

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Bullous pemphigoid

VersionLevelCodeTermSystem organ class
20.0 PT 10004213 Behcet's syndrome 100000004866
22.1 PT 10083073 Immune-mediated myositis 100000004859
20.0 PT 10034277 Pemphigoid 100000004858
20.0 PT 10002817 Antiphospholipid syndrome 100000004851
23.0 LLT 10083567 Immune-mediated thrombocytopenia 10005329
20.0 PT 10012503 Dermatomyositis 100000004858

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Chugai Pharmaceutical Co. Ltd.

Sponsor organisation
Chugai Pharmaceutical Co. Ltd.
Address
1-1 Nihonbashi-Muromachi 2-Chome, Chuo-ku Chuo-ku
City
Chuo
Postcode
103-8324
Country
Japan

Scientific contact point

Organisation
Chugai Pharmaceutical Co. Ltd.
Contact name
Clinical trials information

Public contact point

Organisation
Chugai Pharmaceutical Co. Ltd.
Contact name
Clinical trials information

Locations

14 EU/EEA countries · 42 investigational sites

By country

CountryMS statusPlanned subjectsSites
Austria Ended 4 1
Bulgaria Ongoing, recruiting 6 3
Croatia Ongoing, recruiting 6 6
Czechia Authorised, recruiting 6 1
France Ongoing, recruiting 6 2
Germany Ongoing, recruiting 7 5
Hungary Ongoing, recruiting 5 2
Italy Ongoing, recruiting 4 3
Netherlands Ongoing, recruiting 6 2
Norway Ongoing, recruiting 4 3
Poland Ongoing, recruiting 10 1
Portugal Authorised, recruiting 6 2
Romania Ongoing, recruiting 10 2
Spain Ongoing, recruiting 7 9
Rest of world
Australia, Canada, Taiwan, United States, Japan
57

Investigational sites

Austria

1 site · Ended
Medical University Of Vienna
Department of Clinical Pharmacology, Waehringer Guertel 18-20, Alsergrund, Vienna

Bulgaria

3 sites · Ongoing, recruiting
Specialized Hospital For Active Treatment Of Hematological Diseases EAD
Clinic of Clinical Hematology, Bulevard Kliment Ohridski 1a, 1797, Sofiya
University Multiprofile Hospital For Active Treatment St. Ivan Rilski EAD
Clinic of Rheumatology, Ulitsa Urvich 13, 1612, Sofia
Umbal - Prof. D-R Stoyan Kirkovich AD
Department of Clinical Hematology, Ulitsa General Stoletov 2, 6003, Stara Zagora

Croatia

6 sites · Ongoing, recruiting
Klinicki bolnicki centar Sestre milosrdnice
Clinic for skin and venereal diseases, Vinogradska Cesta 29, Zagreb, Grad Zagreb
KBC Zagreb
Immunodermatology, Ulica Mije Kispatica 12, Zagreb, Grad Zagreb
Specijalna Bolnica Medico
Dermatology and Venerology, Agaticeva 8, 51000, Rijeka
Specijalna Bolnica Medico
Clinical pharmacology, Agaticeva 8, 51000, Rijeka
Specijalna Bolnica Medico
Hematology, Agaticeva 8, 51000, Rijeka
Specijalna Bolnica Medico
Rheumatology, Agaticeva 8, 51000, Rijeka

Czechia

1 site · Authorised, recruiting
Fakultní nemocnice Královské Vinohrady
NA, Šrobárova 50, 100 00, Praha 10 - Vinohrady

France

2 sites · Ongoing, recruiting
Hopital Universitaire Pitie Salpetriere
Internal Medicine, 47 Boulevard De L Hopital, 75651, Paris Cedex 13
Centre Hospitalier Universitaire De Montpellier
Rheumatology, 80 Avenue Augustin Fliche, 34295, Montpellier Cedex 5

Germany

5 sites · Ongoing, recruiting
Immanuel Klinik Ruedersdorf
Neurologie, Seebad 82, 15562, Rüdersdorf
Universitaetsklinikum Tuebingen AöR
Hautklinik, Liebermeisterstrasse 25, Innenstadt, Tuebingen
Technische Universitaet Dresden
Klinik und Poliklinik f. Dermatologie, Fetscherstrasse 74, Johannstadt-Nord, Dresden
Universitaetsmedizin Goettingen
Klinik für Neurologie, Robert-Koch-Strasse 40, Weende, Goettingen
Universitaetsklinikum Erlangen AöR
Hautklinik, Ulmenweg 18, Innenstadt, Erlangen

Hungary

2 sites · Ongoing, recruiting
Semmelweis University
Belgyógyászati és Onkológiai Klinika, Koranyi Sandor Utca 2/a, Kerulet, Budapest VIII
University Of Szeged
Szent-Györgyi Albert Klinikai Központ, Klinikai Farmakológiai Központ Fázis I. vizsgálóhely, Koranyi Fasor 6, 6720, Szeged

Italy

3 sites · Ongoing, recruiting
Istituto Romagnolo Per Lo Studio Dei Tumori Dino Amadori IRST S.r.l.
Oncologia ed Ematologia Clinica e Sperimentale, Via Piero Maroncelli 40, 47014, Meldola
Ospedale San Giovanni Bosco
SCdU Nefrologia e Dialisi, Piazza Del Donatore Di Sangue 3, 10154, Turin
Humanitas Mirasole S.p.A.
Dermatology, Via Alessandro Manzoni 56, 20089, Rozzano

Netherlands

2 sites · Ongoing, recruiting
Universitair Medisch Centrum Groningen
Hematology, Hanzeplein 1, 9713 GZ, Groningen
Universitair Medisch Centrum Utrecht
Hematology, Heidelberglaan 100, 3584 CX, Utrecht

Norway

3 sites · Ongoing, recruiting
Sykehuset Ostfold HF
Hematology, Kalnesveien 300, 1714, Graalum
Sorlandet Sykehus HF
Rheumatology, Egsveien 100, 4615, Kristiansand S
Helse Stavanger HF
Department of Rheumatology, Gerd-Ragna Bloch Thorsens Gate 8, 4011, Stavanger

Poland

1 site · Ongoing, recruiting
Narodowy Instytut Geriatrii Reumatologii I Rehabilitacji Im Prof. Dr Hab. Med. Eleonory Reicher
Centrum Wsparcia Badań Klinicznych, Ul. Spartanska 1, 02-637, Warsaw

Portugal

2 sites · Authorised, recruiting
CCAB Centro Clinico Academico Braga Associacao
Rheumatology, Lugar De Sete Fontes S Victor, 4710-243, Braga
Unidade Local De Saude De Gaia/Espinho E.P.E.
Rheumatology, Rua Conceicao Fernandes S/n, 4434-502, Vila Nova De Gaia

Romania

2 sites · Ongoing, recruiting
Arensia Clinics S.R.L.
Internal Medcine, Intrarea Tudor Stefan 38-40, 011658, Bucharest
Institute Of Oncology Prof. Dr. Ion Chiricuta Cluj-Napoca
Hematology, Strada Republicii 34-36, 400015, Cluj-Napoca

Spain

9 sites · Ongoing, recruiting
Hospital Universitari Vall D Hebron
Internal Medicine, Passeig De La Vall D'Hebron 119-129, 08035, Barcelona
Hospital Universitario Y Politecnico La Fe
Hematology, Avenida De Fernando Abril Martorell 106, 46026, Valencia
Hospital General Universitario Reina Sofia
Rheumatology, Avenida Menendez Pidal S/n, 14004, Cordoba
Hospital Universitario Ramon Y Cajal
Rheumatology, Carretera Del Colmenar Viejo Km 9 100, Por El Pardo, Madrid
Clinica Universidad De Navarra
Hematology, Avenue Pio XII 36, 31008, Pamplona
Hospital Universitari Vall D Hebron
Hematology, Passeig De La Vall D'Hebron 119-129, 08035, Barcelona
Clinica Universidad De Navarra
Hematology, Calle Marquesado De Santa Marta 1, 28027, Madrid
University Hospital Virgen Del Rocio S.L.
Hematology, Avenida De Manuel Siurot S/n, 41013, Sevilla
Hospital Universitario 12 De Octubre
Rheumatology, Bloque D, Avenida De Cordoba Sn, Madrid

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Austria 2024-12-26 2026-05-19
Bulgaria 2024-11-06 2025-11-20
Croatia 2025-05-01 2025-07-03
Czechia 2025-08-29
France 2024-10-18 2024-11-26
Germany 2024-12-12 2026-02-05
Hungary 2024-10-23 2025-02-18
Italy 2024-12-19 2026-03-12
Netherlands 2024-11-27 2025-05-09
Norway 2025-04-28 2025-10-22
Poland 2024-10-16 2024-11-19
Portugal 2025-06-17
Romania 2024-08-22 2024-09-02
Spain 2024-10-25 2024-12-19

Application history

21 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-03-18 Austria Acceptable
2024-07-08
2024-07-09
2 NON SUBSTANTIAL MODIFICATION NSM-1 2024-07-16 Acceptable
2024-07-08
2024-07-16
3 SUBSTANTIAL MODIFICATION SM-5 2024-07-18 Acceptable 2024-08-20
4 SUBSTANTIAL MODIFICATION SM-3 2024-07-18 Acceptable 2024-07-23
5 SUBSTANTIAL MODIFICATION SM-2 2024-07-19 Acceptable 2024-09-10
6 SUBSTANTIAL MODIFICATION SM-4 2024-07-19 Acceptable 2024-08-23
7 SUBSEQUENT ADDITION OF MSC APP-7 2024-08-28 2024-11-25
8 SUBSEQUENT ADDITION OF MSC APP-8 2024-08-28 Acceptable
2024-07-08
2024-11-21
9 SUBSEQUENT ADDITION OF MSC APP-9 2024-08-28 Acceptable
2024-07-08
2024-11-12
10 SUBSEQUENT ADDITION OF MSC APP-10 2024-08-28 Acceptable
2024-07-08
2024-10-30
11 SUBSTANTIAL MODIFICATION SM-6 2024-09-19 Acceptable 2024-11-26
12 SUBSTANTIAL MODIFICATION SM-7 2024-09-20 Acceptable 2024-11-13
13 SUBSTANTIAL MODIFICATION SM-8 2024-10-07 Acceptable 2024-10-17
14 SUBSTANTIAL MODIFICATION SM-9 2024-10-11 Acceptable 2024-11-08
15 SUBSTANTIAL MODIFICATION SM-10 2024-10-14 Acceptable 2024-11-28
16 SUBSTANTIAL MODIFICATION SM-12 2024-12-02 Austria Acceptable
2025-03-24
2025-03-25
17 SUBSTANTIAL MODIFICATION SM-13 2025-04-09 Acceptable 2025-04-14
18 SUBSTANTIAL MODIFICATION SM-14 2025-05-08 Austria Acceptable
2025-07-14
2025-07-15
19 NON SUBSTANTIAL MODIFICATION NSM-3 2025-08-22 Austria Acceptable
2025-07-14
2025-08-22
20 SUBSTANTIAL MODIFICATION SM-15 2025-09-19 Austria Acceptable
2025-12-22
2025-12-23
21 NON SUBSTANTIAL MODIFICATION NSM-4 2026-02-11 Austria Acceptable
2025-12-22
2026-02-11