Phase 1b Study to Assess the Safety, Tolerability and Pharmacodynamics of PBFT02 in Adult Participants with Frontotemporal Dementia (FTD) and GRN or C9orf72 Mutations

2023-507724-23-00 Protocol PBFT02-001 Phase I and Phase II (Integrated) - First administration to humans Ended

Start 1 Feb 2024 · End 7 May 2026 · Status Ended · 2 EU/EEA countries · 3 sites · Protocol PBFT02-001

Overview

Sponsor-declared trial summary

Phase Phase I and Phase II (Integrated) - First administration to humans
Status Ended
Participants planned 16
Countries 2
Sites 3

FRONTOTEMPORAL DEMENTIA (FTD)

Key facts

Sponsor
Passage Bio Inc.
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Nervous System Diseases [C10]
Trial duration
1 Feb 2024 → 7 May 2026
Decision date (initial)
2023-10-11
Transition trial
Yes
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
Yes

External identifiers

EU CT number
2023-507724-23-00
EudraCT number
2020-004499-17
ClinicalTrials.gov
NCT04747431

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

FRONTOTEMPORAL DEMENTIA (FTD)

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Passage Bio Inc.

Sponsor organisation
Passage Bio Inc.
Address
2005 Market Street Floor 39th
City
Philadelphia
Postcode
19103-7026
Country
United States

Scientific contact point

Organisation
Passage Bio Inc.
Contact name
Clinical Information Desk

Public contact point

Organisation
Passage Bio Inc.
Contact name
Clinical Information Desk

Locations

2 EU/EEA countries · 3 investigational sites

By country

CountryMS statusPlanned subjectsSites
Portugal Ended 2 1
Spain Ended 2 2
Rest of world
United States, Brazil, Canada
12

Investigational sites

Portugal

1 site · Ended
Unidade Local De Saude De Coimbra E.P.E.
Servico de Neurologia, Praceta Professor Mota Pinto, 3004-561, Coimbra

Spain

2 sites · Ended
University Hospital Virgen Del Rocio S.L.
UGC Neurology (Memory Unit), Avenida De Manuel Siurot S/n, 41013, Sevilla
Hospital Universitario Central De Asturias
Neurology, Avenida De Roma S/n, 33011, Oviedo

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Portugal 2024-02-01 2025-02-12 2026-05-07

Application history

8 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-08-31 Portugal Acceptable
2023-09-28
2023-10-11
2 SUBSTANTIAL MODIFICATION SM-2 2023-10-17 Portugal Acceptable
2023-12-13
2023-12-14
3 NON SUBSTANTIAL MODIFICATION NSM-1 2024-04-05 Portugal Acceptable
2023-12-13
2024-04-05
4 SUBSTANTIAL MODIFICATION SM-3 2024-11-04 Portugal Acceptable
2025-02-24
2025-02-25
5 NON SUBSTANTIAL MODIFICATION NSM-2 2025-03-04 Portugal Acceptable
2025-02-24
2025-03-04
6 SUBSEQUENT ADDITION OF MSC APP-6 2025-03-13 Acceptable
2025-02-24
2025-06-04
7 SUBSTANTIAL MODIFICATION SM-4 2025-07-31 Portugal Acceptable
2025-09-15
2025-09-16
8 NON SUBSTANTIAL MODIFICATION NSM-3 2026-05-15 Portugal Acceptable
2025-09-15
2026-05-15