Safety, pharmacokinetics, and preliminary efficacy of BYON4413 in acute myeloid leukemia and myelodysplastic neoplasms.

2023-507781-13-00 Protocol BYON4413.001 Human pharmacology (Phase I) - First administration to humans Ended

Start 24 May 2024 · End 30 Sep 2025 · Status Ended · 3 EU/EEA countries · 9 sites · Protocol BYON4413.001

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - First administration to humans
Status Ended
Participants planned 33
Countries 3
Sites 9

Patients with relapsed/refractory acute myeloid leukemia or myelodysplastic neoplasms

Key facts

Sponsor
Byondis B.V.
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Neoplasms [C04], Diseases [C] - Hemic and Lymphatic Diseases [C15]
Trial duration
24 May 2024 → 30 Sep 2025
Decision date (initial)
2024-04-30
Transition trial
No
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
Yes

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Patients with relapsed/refractory acute myeloid leukemia or myelodysplastic neoplasms

VersionLevelCodeTermSystem organ class
21.1 PT 10000880 Acute myeloid leukaemia 100000004864
21.1 PT 10028533 Myelodysplastic syndrome 100000004864

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Byondis B.V.

Sponsor organisation
Byondis B.V.
Address
Microweg 22
City
Nijmegen
Postcode
6545 CM
Country
Netherlands

Scientific contact point

Organisation
Byondis B.V.
Contact name
Clinical Development

Public contact point

Organisation
Byondis B.V.
Contact name
Clinical Development

Locations

3 EU/EEA countries · 9 investigational sites

By country

CountryMS statusPlanned subjectsSites
Belgium Ended 8 2
Netherlands Ended 4 1
Spain Ended 21 6
Rest of world 0

Investigational sites

Belgium

2 sites · Ended
Het Ziekenhuisnetwerk Antwerpen
Hematology, Kempenstraat 100, 2030, Antwerp
UZ Leuven
Hematology, Herestraat 49, 3000, Leuven

Netherlands

1 site · Ended
Universitair Medisch Centrum Groningen
Hematology, Hanzeplein 1, 9713 GZ, Groningen

Spain

6 sites · Ended
Institut Catala D'oncologia
Servicio de Hematología, Carretera Canyet S/n, 08916, Badalona
Hospital De La Santa Creu I Sant Pau
Servicio de Hematología, Carrer De San Quinti 89, 08041, Barcelona
Hospital Universitario De Salamanca
Servicio de Hematología, Paseo De San Vicente 58-182, 37007, Salamanca
Hospital Universitario Y Politecnico La Fe
Servicio de Hematología, Avenida De Fernando Abril Martorell 106, 46026, Valencia
Hospital Clinic De Barcelona
Servicio de Hematología, Calle Villarroel 170, 08036, Barcelona
Hospital San Pedro De Alcantara
Servicio de Hematología, Avenida De Pablo Naranjo Porras S/n, 10002, Caceres

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Belgium 2024-06-13 2024-07-29 2024-12-17
Netherlands 2024-06-10 2024-09-20 2025-08-20
Spain 2024-05-24 2024-06-17 2025-09-22

Application history

2 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-12-22 Spain Acceptable
2024-04-29
2024-04-30
2 SUBSTANTIAL MODIFICATION SM-1 2025-07-23 Spain Acceptable
2025-09-16
2025-09-17