Meningococcal B vaccine in patients with asplenia

2023-508192-36-00 Protocol MenB_Asplenia Therapeutic exploratory (Phase II) Ongoing, recruitment ended

Start 5 Mar 2024 · Status Ongoing, recruitment ended · 1 EU/EEA countries · 1 sites · Protocol MenB_Asplenia

Overview

Sponsor-declared trial summary

Phase Therapeutic exploratory (Phase II)
Status Ongoing, recruitment ended
Participants planned 80
Countries 1
Sites 1

Splenectomy

To demonstrate that the immunogenicity of the meningococcal serogroup B vaccine BEXSERO® is non-inferior in asplenic patients compared to a healthy control group, measured by human serum bactericidal antibody assay one month after second vaccination.

Key facts

Sponsor
Medical University of Vienna
Participant type
Healthy volunteers, Patients
Age range
18-64 years
Gender
Male and Female
Therapeutic area
Diseases [C] - Bacterial Infections and Mycoses [C01]
Trial duration
5 Mar 2024 → ongoing
Decision date (initial)
2024-02-05
Transition trial
No
Low-intervention
Yes
Rare-disease indication
No
Vulnerable population
No
Funding sources
Austrian Science Fund

External identifiers

EU CT number
2023-508192-36-00
WHO UTN
U1111-1297-8468
ClinicalTrials.gov
NCT06025487

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Others

To demonstrate that the immunogenicity of the meningococcal serogroup B vaccine BEXSERO® is non-inferior in asplenic patients compared to a healthy control group, measured by human serum bactericidal antibody assay one month after second vaccination.

Secondary objectives 3

  1. To assess the persistence of antibodies six months after second vaccination in asplenic patients compared to healthy controls.
  2. To assess the cellular immune response by lymphocyte proliferation assay and measurement of interleukins in asplenic patients compared to healthy controls at baseline and one month after second vaccination.
  3. To assess the safety of the vaccine in asplenic patients

Conditions and MedDRA coding

Splenectomy

VersionLevelCodeTermSystem organ class
20.0 PT 10041642 Splenectomy 100000004865

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 4

  1. asplenia due to splenectomy or functional asplenia (only patients)
  2. 18 to 60 years of age
  3. if female: have a negative urine pregnancy test result at study entry and agree to employ adequate birth control measures for the duration of the study
  4. providing written informed consent

Exclusion criteria 7

  1. previous vaccination against meningococcal serogroup B
  2. pregnant or lactating
  3. febrile illness within last two weeks prior to enrolment
  4. allergic reactions to vaccination in past
  5. chemotherapy with Rituximab within last six months or during study period (only patients)
  6. more than 20mg prednisone per day within last four weeks prior or at the time of enrolment (only patients)
  7. any immunosuppressive condition or medication (only healthy controls)

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. The primary end point is the mean log-titre over the three meningococcal strains (NZ98/254 for PorA, 5/99 for NadA and 44/76-SL for fHbp) as measured by the hSBA one month after second vaccination. The non-inferiority margin was set to a 2-fold titre difference between the geometric mean titre of the asplenic group and the healthy control group.

Secondary endpoints 3

  1. The persistence of antibodies will be measured six months after second vaccination and the difference between the means of the log-titers between the asplenic and the control group will be calculated.
  2. The cellular immune response as measured by lymphocyte proliferation assay and cytokine levels.
  3. Adverse events (AEs) during the observation period will be tabulated by single events with the number of the vaccination, the type of the event, its severity and evaluation concerning its relation to the vaccination, potential treatment and sequelae.

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 1

Bexsero suspension for injection in pre-filled syringe Meningococcal group B Vaccine (rDNA, component, adsorbed)

PRD2149122 · Product

Active substance
Recombinant Neisseria Meningitidis Group B Nhba Fusion Protein Produced in E. Coli Cells by Recombinant DNA Technology Adsorbed on Aluminium Hydroxide
Pharmaceutical form
SUSPENSION FOR INJECTION
Route of administration
INTRAMUSCULAR INJECTION
Max daily dose
0.5 ml millilitre(s)
Max total dose
1 ml millilitre(s)
Max treatment duration
5 Week(s)
Authorisation status
Authorised
ATC code
J07AH09 — -
Marketing authorisation
EU/1/12/812/001
MA holder
GSK VACCINES S.R.L.
MA country
Liechtenstein
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Medical University of Vienna

Sponsor organisation
Medical University of Vienna
Address
Waehringer Guertel 18-20, Alsergrund Alsergrund
City
Vienna
Postcode
1090
Country
Austria

Scientific contact point

Organisation
Medical University of Vienna
Contact name
Department of Medicine I Division of Infectious Diseases and Tropical Medicine

Public contact point

Organisation
Medical University of Vienna
Contact name
Department of Medicine I Division of Infectious Diseases and Tropical Medicine

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Austria Ongoing, recruitment ended 80 1
Rest of world 0

Investigational sites

Austria

1 site · Ongoing, recruitment ended
Medical University of Vienna
Department of Medicine I Division of Infectious Diseases and Tropical Medicine, Waehringer Guertel 18-20, Alsergrund, Vienna

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Austria 2024-03-05 2024-03-12 2026-04-09

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 4 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Recruitment arrangements (for publication) K1_Recruitment arrangements_Redacted 1
Subject information and informed consent form (for publication) D4_Patient diary_Redacted 1
Subject information and informed consent form (for publication) L1_SIS and ICF adults_Redacted 5
Subject information and informed consent form (for publication) L2_information poster_Redacted 1

Application history

3 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-10-17 Austria Acceptable
2024-01-12
2024-02-05
2 NON SUBSTANTIAL MODIFICATION NSM-3 2024-02-15 Austria Acceptable
2024-01-12
2024-02-15
3 NON SUBSTANTIAL MODIFICATION NSM-4 2025-01-02 Austria Acceptable
2024-01-12
2025-01-02