A Phase 1, multicenter, open-label study of REM-422, a MYB mRNA degrader, in patients with recurrent or metastatic, adenoid cystic carcinoma.

2023-508476-11-00 Protocol REM-422-101 Human pharmacology (Phase I) - First administration to humans Authorised, recruitment pending

Status Authorised, recruitment pending · 1 EU/EEA countries · 5 sites · Protocol REM-422-101

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - First administration to humans
Status Authorised, recruitment pending
Participants planned 100
Countries 1
Sites 5

Adenoid cystic carcinoma (ACC)

Key facts

Sponsor
Remix Therapeutics Inc.
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Neoplasms [C04]
Decision date (initial)
2024-05-06
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
Yes

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Adenoid cystic carcinoma (ACC)

VersionLevelCodeTermSystem organ class
21.0 PT 10053231 Adenoid cystic carcinoma 100000004864

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Remix Therapeutics Inc.

Sponsor organisation
Remix Therapeutics Inc.
Address
100 Forge Road Suite 400
City
Watertown
Postcode
02472-2265
Country
United States

Scientific contact point

Organisation
Remix Therapeutics Inc.
Contact name
Jennifer Webster

Public contact point

Organisation
Remix Therapeutics Inc.
Contact name
Jennifer Webster

Locations

1 EU/EEA country · 5 investigational sites

By country

CountryMS statusPlanned subjectsSites
France Authorised, recruitment pending 30 5
Rest of world
United States
70

Investigational sites

France

5 sites · Authorised, recruitment pending
Institut Gustave Roussy
Cancérologie Cervico-Faciale, 114 Rue Edouard Vaillant, 94800, Villejuif
Centre Hospitalier Universitaire De Bordeaux
Oncologie Médicale, 1 Rue Jean Burguet, 33000, Bordeaux
Institut De Cancerologie De L Ouest
Oncologie Médicale, Bd Du Professeur Jacques Monod, 44800, St Herblain
Centre Antoine Lacassagne
Unité de Phase Précoce, 33 Avenue De Valombrose, 06189, Nice Cedex 2
Centre Leon Berard
Oncologie Médicale, 28 Rue Laennec, 69008, Lyon

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
France

Application history

8 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-01-29 France Acceptable with conditions
2024-04-29
2024-05-06
2 SUBSTANTIAL MODIFICATION SM-1 2025-01-15 France Acceptable
2025-02-14
2025-02-26
3 SUBSTANTIAL MODIFICATION SM-2 2025-03-18 France Acceptable
2025-05-14
2025-05-14
4 SUBSTANTIAL MODIFICATION SM-3 2025-05-14 France Acceptable
2025-07-15
2025-07-15
5 SUBSTANTIAL MODIFICATION SM-4 2025-07-29 France Acceptable
2025-08-29
2025-08-29
6 NON SUBSTANTIAL MODIFICATION NSM-1 2025-11-26 France Acceptable
2025-08-29
2025-11-26
7 SUBSTANTIAL MODIFICATION SM-6 2026-02-12 France Acceptable with conditions
2026-04-17
2026-04-17
8 SUBSTANTIAL MODIFICATION SM-7 2026-04-24 France Acceptable with conditions 2026-05-13