Study to assess the safety, pharmacokinetics and efficacy of HMPL-523 in patients with Immune Thrombocytopenia

2023-508819-23-00 Protocol 2022-523-GLOB1 Human pharmacology (Phase I) - Other Ended

Start 24 Jul 2024 · End 19 May 2025 · Status Ended · 3 EU/EEA countries · 15 sites · Protocol 2022-523-GLOB1

Overview

Sponsor-declared trial summary

Phase Human pharmacology (Phase I) - Other
Status Ended
Participants planned 55
Countries 3
Sites 15

Primary immune thrombocytopenia (ITP)

Key facts

Sponsor
Hutchmed Ltd.
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Hemic and Lymphatic Diseases [C15]
Trial duration
24 Jul 2024 → 19 May 2025
Decision date (initial)
2024-08-30
Transition trial
No
Low-intervention
No
Rare-disease indication
Yes
Vulnerable population
No

Trial design

CTIS Part I — objectives, methods, condition coding

Conditions and MedDRA coding

Primary immune thrombocytopenia (ITP)

VersionLevelCodeTermSystem organ class
23.0 LLT 10083843 Primary immune thrombocytopenia 10005329

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Hutchmed Ltd.

Sponsor organisation
Hutchmed Ltd.
Address
Building 4, 720 Cailun Road, China (Shanghai) Pilot Free Trade Zone 720 Cailun Road China (Shanghai) Pilot Free Trade Zone
City
Shanghai
Postcode
201203
Country
China

Scientific contact point

Organisation
Hutchmed Ltd.
Contact name
Clinical Trial Information

Public contact point

Organisation
Hutchmed Ltd.
Contact name
Clinical Trial Information

Locations

3 EU/EEA countries · 15 investigational sites

By country

CountryMS statusPlanned subjectsSites
Germany Ended 7 4
Norway Ended 3 2
Spain Ended 12 9
Rest of world
Australia, United States
33

Investigational sites

Germany

4 sites · Ended
Universitaetsmedizin Goettingen
Department of Hematology and Medical Oncology, Robert-Koch-Strasse 40, Weende, Goettingen
Universitaetsklinikum Schleswig-Holstein AöR
Klinik for Hematology and Oncology, Ratzeburger Allee 160, 23538, Luebeck
Charite Universitaetsmedizin Berlin KöR
Department of Hematology, Oncology and Tumorimmunology, Hindenburgdamm 30, Lichterfelde, Berlin
Marien Hospital Duesseldorf GmbH
Klinik für Onkologie, Hämatologie und Palliativmedizin, Rochusstrasse 2, Pempelfort, Duesseldorf

Norway

2 sites · Ended
Ostfold Hospital Trust
Department of Research, P. O. Box 16, 1603, Fredrikstad
Oslo University Hospital HF
Department of Haematology, Sognsvannsveien 20, 0372, Oslo

Spain

9 sites · Ended
Clinica Universidad De Navarra
Hematology, Avenue Pio XII 36, 31008, Pamplona
Hospital Universitario De Burgos
Hematology, Avenida De Las Islas Baleares 3, 09006, Burgos
Hospital Universitari Vall D Hebron
Hematology, Edificio Materno-Infantil, Passeig De La Vall D'hebron 119-129, Barcelona
Hospital Del Mar
Hematology, Passeig Maritim De La Barceloneta 25-29, 08003, Barcelona
Clinica Universidad De Navarra
Hematology, Calle Marquesado De Santa Marta 1, 28027, Madrid
Hospital Universitario Fundacion Jimenez Diaz
Hematology, Avenida De Los Reyes Catolicos 2, 28040, Madrid
Hospital General Universitario Morales Meseguer
Hematology, Avenida Del Marques De Los Velez S/n, 30008, Murcia
Hospital Universitario Infanta Leonor
Hematology, Avenida Gran Via Del Este 80, 28031, Madrid
Hospital General Universitario Gregorio Maranon
Hematology, Calle Del Doctor Esquerdo 46, 28009, Madrid

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Norway 2024-08-08
Spain 2024-07-24

Application history

4 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-03-01 Norway Acceptable
2024-06-03
2024-06-05
2 SUBSTANTIAL MODIFICATION SM-1 2024-06-14 Norway Acceptable 2024-06-25
3 SUBSEQUENT ADDITION OF MSC APP-3 2024-06-14 Acceptable
2024-06-03
2024-08-30
4 SUBSTANTIAL MODIFICATION SM-2 2024-11-18 Norway Acceptable
2025-01-15
2025-01-15