Testing LADA diabetes status 3 years after treatment with intranodal GAD-alum.

2023-509021-53-00 Therapeutic exploratory (Phase II) Ongoing, recruitment ended

Start 5 Jun 2024 · Status Ongoing, recruitment ended · 2 EU/EEA countries · 2 sites

Overview

Sponsor-declared trial summary

Phase Therapeutic exploratory (Phase II)
Status Ongoing, recruitment ended
Participants planned 14
Countries 2
Sites 2

Latent Autoimmune Diabetes in Adults (LADA)

The main objective is to test for possible differences in current diabetes status (assessed by measurements of beta cell function and metabolic control) between carriers and non-carriers of HLA-DR3DQ2, 3 years after treatment with GAD-alum in our previous GADinLADA study.

Key facts

Sponsor
Norwegian University Of Science And Technolology
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Immune System Diseases [C20]
Trial duration
5 Jun 2024 → ongoing
Decision date (initial)
2024-05-03
Transition trial
No
Low-intervention
No
Rare-disease indication
No
Vulnerable population
No

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Therapy

The main objective is to test for possible differences in current diabetes status (assessed by measurements of beta cell function and metabolic control) between carriers and non-carriers of HLA-DR3DQ2, 3 years after treatment with GAD-alum in our previous GADinLADA study.

Conditions and MedDRA coding

Latent Autoimmune Diabetes in Adults (LADA)

VersionLevelCodeTermSystem organ class
20.0 LLT 10072399 LADA 10027433

Regulatory references

Plan to share IPD
No
EU CT numberTitleSponsor
2019-002692-34 A pilot study on safety, feasibility and insulin-promotion by intra-inguinal lymph node injections of glutamic acid decarboxylase (GAD) in patients with LADA type of diabetes.

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 2

  1. Signed informed consent
  2. Former participant in the GADinLADA study (EudraCT 2019-002692-34)

Exclusion criteria 2

  1. Presence of serious disease or condition (including pregnancy)
  2. Participation in other clinical trials, which in the opinion of the investigator makes the patient non-eligible for the project

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Change in diabetes status variables (beta cell insulin secretion capacity and metabolic control) 3 years after treatment with GAD-alum (IMP) in the GADinLADA study, compared to baseline and the end of study (i.e., 12 months after baseline) in GADinLADA.

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 1

Diamyd

PRD221979 · Product

Active substance
Glutamate Decarboxylase 2, Human, Recombinant
Pharmaceutical form
SUSPENSION FOR INJECTION
Route of administration
INTRALYMPHATIC USE
Max daily dose
0 µg microgram(s)
Max total dose
0 µg microgram(s)
Max treatment duration
1 Day(s)
Authorisation status
Not Authorised
MA holder
DIAMYD MEDICAL AB
Paediatric formulation
No
Orphan designation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Norwegian University Of Science And Technolology

Sponsor organisation
Norwegian University Of Science And Technolology
Address
Hoegskoleringen 1
City
Trondheim
Postcode
7034
Country
Norway

Scientific contact point

Organisation
Norwegian University Of Science And Technolology
Contact name
Dept. of clinical an molecular medicine

Public contact point

Organisation
Norwegian University Of Science And Technolology
Contact name
Dept. of clinical an molecular medicine

Locations

2 EU/EEA countries · 2 investigational sites

By country

CountryMS statusPlanned subjectsSites
Norway Ongoing, recruitment ended 6 1
Sweden Ongoing, recruitment ended 8 1
Rest of world 0

Investigational sites

Norway

1 site · Ongoing, recruitment ended
Norwegian University Of Science And Technolology
Department of clinical and molecular medicine, Hoegskoleringen 1, 7034, Trondheim

Sweden

1 site · Ongoing, recruitment ended
Karolinska Institutet
Department of Molecular Medicine and Surgery, Nobels Vag 6, 171 65, Solna

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Norway 2024-06-05 2024-06-14 2025-11-30
Sweden 2024-12-17 2025-01-07 2025-11-30

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 18 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) D1_ Protocol_2023-509021-53-00_For publication 3
Protocol (for publication) D1_ Protocol_2023-509021-53-00_Public_Version 2_Final 2
Recruitment arrangements (for publication) K1_ Recruitment arrangements_Norway 1
Recruitment arrangements (for publication) K1_ Recruitment arrangements_Norway_V2 2
Recruitment arrangements (for publication) K1_Recruitment arrangements_V4_Final_SE 4
Recruitment arrangements (for publication) K1_Recruitment arrangementsV2_SE 3
Subject information and informed consent form (for publication) L1_ SIS and ICF adults_Norway_public 1
Subject information and informed consent form (for publication) L1_ SIS and ICF adults_Norway_Public_Version 2 3
Subject information and informed consent form (for publication) L1_ SIS and ICF adults_Sweden_Public 1
Subject information and informed consent form (for publication) L1_ SIS and ICF adults_Sweden_Public_V2 2
Subject information and informed consent form (for publication) L1_ SIS and ICF adults_Sweden_Public_V3 3
Subject information and informed consent form (for publication) L1_ SIS and ICF adults_Sweden_Public_V4 4
Subject information and informed consent form (for publication) L1_ SIS and ICF adults_Sweden_Public_V5 5
Subject information and informed consent form (for publication) L1_SIS and ICF adults_Limited Participation_Norway_Version 4_25April2025_Final_Public 4
Summary of Product Characteristics (SmPC) (for publication) G2_ SmPC rhGAD65 Placeholder document 1
Synopsis of the protocol (for publication) D1_ Protocol synopsisV1_SE 2023-509021-53-00 1
Synopsis of the protocol (for publication) D1_ Protocol synopsisV2_ENG 2023-509021-53-00 2
Synopsis of the protocol (for publication) D1_ Protocol synopsisV2_NO 2023-509021-53-00 2

Application history

8 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2024-02-09 Norway Acceptable
2024-05-03
2024-05-03
2 NON SUBSTANTIAL MODIFICATION NSM-1 2024-05-20 Norway Acceptable
2024-05-03
2024-05-20
3 NON SUBSTANTIAL MODIFICATION NSM-2 2024-05-27 Acceptable
2024-05-03
2024-05-27
4 SUBSTANTIAL MODIFICATION SM-1 2024-05-27 Norway Acceptable 2024-06-03
5 NON SUBSTANTIAL MODIFICATION NSM-3 2024-06-13 Norway Acceptable 2024-06-13
6 NON SUBSTANTIAL MODIFICATION NSM-4 2024-07-08 Acceptable 2024-07-08
7 NON SUBSTANTIAL MODIFICATION NSM-5 2025-04-25 Norway Acceptable 2025-04-25
8 SUBSTANTIAL MODIFICATION SM-2 2025-05-15 Norway Acceptable
2025-07-17
2025-07-17