30% or 60% Oxygen at Birth to Improve Neurodevelopmental Outcomes in Very Low Birthweight Infants

2023-509780-25-00 Protocol Pro00083931 Therapeutic confirmatory (Phase III) Ongoing, recruiting

Start 9 Oct 2024 · Status Ongoing, recruiting · 1 EU/EEA countries · 1 sites · Protocol Pro00083931

Overview

Sponsor-declared trial summary

Phase Therapeutic confirmatory (Phase III)
Status Ongoing, recruiting
Participants planned 1,250
Countries 1
Sites 1

Prematurity

The null hypothesis for this study is that the incidence of mortality or abnormal neurodevelopmental outcomes at 18-24 months corrected age will be no different by using either higher initial oxygen concentration of 60% compared to using lower initial oxygen concentration of 30% for resuscitation of preterm infants of …

Key facts

Sponsor
University College Cork
Participant type
Pediatric, Patients
Age range
0-17 years
Gender
Male and Female
Therapeutic area
Diseases [C] - Congenital, Hereditary, and Neonatal Diseases and Abnormalities [C16]
Trial duration
9 Oct 2024 → ongoing
Decision date (initial)
2024-05-03
Transition trial
No
Low-intervention
Yes
Rare-disease indication
No
Vulnerable population
Yes
Funding sources
Canadian Institute of Health Research Foundation Grant (CIHR)

External identifiers

EU CT number
2023-509780-25-00
ClinicalTrials.gov
NCT03825835

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Therapy, Safety, Efficacy

The null hypothesis for this study is that the incidence of mortality or abnormal neurodevelopmental outcomes at 18-24 months corrected age will be no different by using either higher initial oxygen concentration of 60% compared to using lower initial oxygen concentration of 30% for resuscitation of preterm infants of 23-28 weeks’ gestation.

Conditions and MedDRA coding

Prematurity

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 3

  1. Infants with gestational age between 23 to 28 weeks based on best available obstetrical estimate
  2. Infants designated to receive full resuscitation, i.e., no parental request or pre-determined decision to forego resuscitation
  3. No known major congenital or chromosomal malformation.

Exclusion criteria 2

  1. Infant born outside of study centers and transported to center after delivery
  2. Parents’ refusal to give consent to this study

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. The primary outcome is a composite between 18 and 24 months corrected age of all-cause mortality or the presence of a major neurodevelopmental outcome defined as any one of: (i) non-ambulatory cerebral palsy; (ii) severe cognitive delay, (iii) hearing impairment (requiring a hearing aid or cochlear implants), and (iv) visual (cannot fixate/ legally blind, or corrected acuity <6/60 in both eyes).

Secondary endpoints 4

  1. All-cause in-hospital mortality
  2. Severe brain injury, defined as Grade 3 and 4 IVH / intraparenchymal hemorrhage or echodense intraparenchymal lesions, periventricular leukomalacia, porencephalic cysts or ventriculomegaly on cranial ultrasound
  3. Bronchopulmonary dysplasia
  4. Severe retinopathy of prematurity (stage 3 or 4 or treated cases)

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 1

Medical Oxygen

PRD404326 · Product

Active substance
Oxygen Ph.eur.
Pharmaceutical form
MEDICINAL GAS, COMPRESSED
Route of administration
INHALATION GAS
Max daily dose
100 % percent
Max total dose
100 % percent
Max treatment duration
1 Day(s)
Authorisation status
Authorised
ATC code
V03AN01 — -
Marketing authorisation
PA 0208/003/001
MA holder
BOC GASES IRELAND LTD
MA country
Ireland
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

University College Cork

Sponsor organisation
University College Cork
Address
6 Little Hanover Street
City
Cork
Postcode
T12 E30P
Country
Ireland

Scientific contact point

Organisation
University College Cork
Contact name
Muiris Dowling

Public contact point

Organisation
University College Cork
Contact name
Study Manager

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Ireland Ongoing, recruiting 65 1
Rest of world
Canada
1,185

Investigational sites

Ireland

1 site · Ongoing, recruiting
Cork University Maternity Hospital
Paediatrics and Child Health, Wilton Road, T12 YE02, Cork

Country notifications

Trial-start, recruitment-start, end and early-termination notifications submitted per Member State

Country Trial startTrial end Recruitment startRecruitment end Early termination
Ireland 2024-10-09 2024-10-24

Results and documents

Annex IV summary of results, Annex V layperson summary, and all documents registered in CTIS for this trial

Documents 5 files

Public protocol annexes, IB summaries, regulatory submissions and post-authorisation documents registered in CTIS.

TypeTitleVersion
Protocol (for publication) D1 HiLo Protocol 2023-509780-25-00 3.8
Protocol (for publication) D1 Protocol_GSA_IRE_2023-509780-25-00 1
Recruitment arrangements (for publication) K1_Recruitment Arrangements 1
Subject information and informed consent form (for publication) L1_HiLo ICF_IE 4.0
Summary of Product Characteristics (SmPC) (for publication) E1_SmPC Medical Oxygen 1

Application history

3 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-12-21 Ireland Acceptable
2024-04-29
2024-05-03
2 NON SUBSTANTIAL MODIFICATION NSM-1 2024-10-01 Ireland Acceptable
2024-04-29
2024-10-01
3 SUBSTANTIAL MODIFICATION SM-4 2026-02-10 Ireland Acceptable
2026-04-20
2026-04-20