The role of meldonium and individualized physical activities in the treatment of patients with heart failure

2023-509804-14-00 Protocol MELD-PHYS-2023 Therapeutic use (Phase IV) Authorised, recruitment pending

Status Authorised, recruitment pending · 1 EU/EEA countries · 1 sites · Protocol MELD-PHYS-2023

Overview

Sponsor-declared trial summary

Phase Therapeutic use (Phase IV)
Status Authorised, recruitment pending
Participants planned 200
Countries 1
Sites 1

Chronic heart failure with preserved ejection fraction

To evaluate effectiveness of meldonium and individualised physical activity recommendations in patients with heart failure with preserved ejection fraction.

Key facts

Sponsor
Pauls Stradins Clinical University Hospital
Participant type
Patients
Age range
18-64 years, 65+ years
Gender
Male and Female
Therapeutic area
Diseases [C] - Cardiovascular Diseases [C14]
Decision date (initial)
2024-03-27
Transition trial
No
Low-intervention
Yes
Rare-disease indication
No
Vulnerable population
Yes

Trial design

CTIS Part I — objectives, methods, condition coding

Main objective

Scope: Prophylaxis

To evaluate effectiveness of meldonium and individualised physical activity recommendations in patients with heart failure with preserved ejection fraction.

Conditions and MedDRA coding

Chronic heart failure with preserved ejection fraction

Eligibility criteria

Principal inclusion / exclusion criteria as submitted by sponsor

Inclusion criteria 5

  1. Chronic heart failure II - III functional class NYHA (The New York Heart Association)
  2. In transthoracic echocardiography calculated left ventricle ejection fraction >50 un LAVI >34 ml/m2.
  3. Patient receives optimal medical therapy for at least 3 months.
  4. Coronary angiography or computed coronary angiography has been done to rule out obstructive coronary artery disease
  5. Patients ≥18 years

Exclusion criteria 9

  1. Allergic reaction to meldonium
  2. Patient is involved in other trial
  3. Iron deficiency anemia (men Hb < 13 g/dL, women Hb <12 g/dl un serum ferritin levels < 30ng/ml or transferrin saturation ≤19 %)
  4. Severe kindey or liver disfunction
  5. Congenital heart diseases
  6. Moderate to severe cardiac valve diseases
  7. Pregnancy/breastfeeding women
  8. Patient uses digoxin, trimetazidine, ranolazine, meldonium, ivabradine
  9. Patient underwent coronary revascularisation within 3 months

Endpoints

Primary and secondary outcome measures (English text)

Primary endpoints 1

  1. Physical activity tolerance change asessed by the cardiopulmonary test (relative maximal oxygen uptake, VO2 max ml/min/kg)

Investigational products

Investigational medicinal products (IMPs), comparators, placebo, auxiliary

Test 1

Meldonium

SUB30147 · Substance

Active substance
Meldonium
Pharmaceutical form
CAPSULE
Route of administration
ORAL
Max daily dose
1000 mg milligram(s)
Max total dose
1000 mg milligram(s)
Max treatment duration
6 Week(s)
Authorisation status
Authorised
ATC code
- — -
Marketing authorisation
-
Paediatric formulation
No
Orphan designation
No
Modified vs. Marketing Authorisation
No

Sponsors and contacts

Sponsor organisations, regulatory contacts, third parties

Pauls Stradins Clinical University Hospital

Sponsor organisation
Pauls Stradins Clinical University Hospital
Address
Pilsonu Iela 13
City
Riga
Postcode
1002
Country
Latvia

Scientific contact point

Organisation
Pauls Stradins Clinical University Hospital
Contact name
Head of clinical trials

Public contact point

Organisation
Pauls Stradins Clinical University Hospital
Contact name
Head of clinical trials

Locations

1 EU/EEA country · 1 investigational sites

By country

CountryMS statusPlanned subjectsSites
Latvia Authorised, recruitment pending 200 1
Rest of world 0

Investigational sites

Latvia

1 site · Authorised, recruitment pending
Pauls Stradins Clinical University Hospital
Invasive cardiology, Pilsonu Iela 13, 1002, Riga

Application history

1 submissions — initial application plus substantial / non-substantial modifications

#TypeCodeSubmittedReference MSConclusionDecision date
1 INITIAL IN 2023-12-08 Latvia Acceptable
2024-03-25
2024-03-27